This multicenter, multinational, longitudinal study will quantify endurance and respiratory function in subjects diagnosed with MPS IVA and will better characterize the spectrum of symptoms and biochemical abnormalities in MPS IVA disease over time.
Study Type
OBSERVATIONAL
Enrollment
353
Unnamed facility
Oakland, California, United States
Unnamed facility
Chicago, Illinois, United States
Unnamed facility
Córdoba, Argentina
Unnamed facility
Porto Alegre, Brazil
Endurance
Time frame: Study Visit
Respiratory Function
Time frame: Study Visit
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Unnamed facility
São Paulo, Brazil
Unnamed facility
Montreal, Quebec, Canada
Unnamed facility
Lyon, France
Unnamed facility
Paris, France
Unnamed facility
Mainz, Germany
Unnamed facility
Monza, Italy
...and 5 more locations