Cardiac Outcome Measures in Children With Muscular Dystrophy

Cooperative International Neuromuscular Research Group48 enrolled

Overview

The purpose of the research study is to evaluate different cardiac measures that are obtained by echocardiographic tests in patients with muscular dystrophy.

The research study will include 50 participants aged 8 to 18 years old (before 18th birthday) with Duchenne, Becker, or autosomal recessive limb-girdle (specifically: LGMD 2C-2F and 2I) muscular dystrophies. Participants will be seen in one of five Cooperative International Neuromuscular Research Group (CINRG) centers located in the United States. All study assessments will be completed in the same day and include reviewing past medical and surgical history, collecting vital signs, collecting cardiac measures through echocardiographic tests.

Study Type

OBSERVATIONAL

Enrollment

Conditions

Duchenne Muscular Dystrophy Becker Muscular Dystrophy Limb Girdle Muscular Dystrophy

Eligibility

Sex: ALLMin age: 8 YearsMax age: 18 Years

Medical Language ↔ Plain English

Inclusion Criteria: * Participants must be between the ages of 8 and 18 years old * Confirmed diagnosis of muscular dystrophy (DMD, BMD, or LGMD 2C-2F and 2I) Exclusion Criteria: * Investigator assessment of inability to comply with protocol * History of a congenital cardiac defect or other cardiac disease unrelated to muscular dystrophy

Locations (5)

University of California Davis

Sacramento, California, United States

Children's National Medical Center

Washington D.C., District of Columbia, United States

Washington University St. Louis

St Louis, Missouri, United States

University of Pittsburgh

Pittsburgh, Pennsylvania, United States

Data from ClinicalTrials.gov

This platform is for informational purposes only and does not constitute medical advice. Always consult a qualified healthcare professional.