The purpose of this study is to proof increasing patient satisfaction and preservation of quality of life in patients with Gaucher's Disease receiving their enzyme replacement therapy with VPRIV (Velaglucerase alfa)at their home setting compared to receiving the infusions at the clinic or at doctor's practice.
Study Type
OBSERVATIONAL
Enrollment
34
Landeskrankenhaus Bregenz
Bregenz, Austria
Paracelsus Medizinische Privatuniversität Salzburg
Salzburg, Austria
AKH, Allgemeines Krankenhaus der Stadt Wien
Vienna, Austria
Patient satisfaction estimated on a 10-ary Likert scale, quality of life estimated by SF-36 questionnaire
Time frame: comparison of baseline to 12 months value
Number (per infusion) and severity of infusion-related side effects
Time frame: baseline compared to 12 months
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Medical University of Vienna
Vienna, Austria
Medizinische Universität Wien
Vienna, Austria
Gemeinschaftspraxis für Hämatologie und Onkologie
Cologne, Germany
Universitätsklinikum Mainz
Mainz, Germany
Klinikum rechts der Isar
München, Germany
Albrecht-Kossel-Institut für Neuroregeneration (AKos)
Rostock, Germany
Helios Klinikum Schwerin
Schwerin, Germany
...and 1 more locations