The purpose of this study is to identify potential biomarkers for the diagnosis, disease progression assessment and response to treatment in patients with Duchenne Muscular Dystrophy.
Study Type
OBSERVATIONAL
Enrollment
220
Institute of Myology
Paris, France
IBiSD aims to identify and validate new and disease-specific biomarkers.
This study will establish the relevance of urinary and blood biomarkers for the diagnosis, follow-up and assessment of treatment response in patients with DMD (IBiSD1, 2 and 4). IBiSD will also attempt to establish the seroprevalence to the different strains of AAV in patients with DMD (IBiSD3).
Time frame: End of study
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