There is limited information on the long-term effects of treating patients with MPS VI with Naglazyme® and limited data on the natural history of treated and untreated MPS VI patients. The Re-survey Study ASB-00-03 will assist in understanding the effects of long-term Naglazyme treatment and the natural history of the MPS VI patient population.
Study Type
OBSERVATIONAL
Enrollment
59
Children's Hospital and Research Center
Oakland, California, United States
Women's and Children's hospital
North Adelaide, Australia
Hospital de Clinicas de Porto Alegre
Porto Alegre, Brazil
Hôpital Femme Mère Enfant
Lyon, Lyon, France
Linear Comparison of assessments completed for Survey Study ASB-00-02 and and Re-Survey StudyASB-00-03
This study is designed to be performed in a similar manner to the Survey Study ASB-00-02. Similar assessments will be performed in order to make linear comparisons in outcomes over a long-term period.
Time frame: Variable dependent on date of assessment performed fo rthe Survey STudy ASB-00-02
This platform is for informational purposes only and does not constitute medical advice. Always consult a qualified healthcare professional.
Prof Michael Beck
Mainz, Mainz, Germany
Al. Prof Hernani Monteiro
Porto, Porto District, Portugal
Manchester Academic Health Sciences Centre
Manchester, Manchester, United Kingdom