The purpose of this study is to explore long-term safety, tolerability and efficacy of GSK2402968 in DMD subjects who previously participated in either DMD114117 or DMD114044.
Study Type
INTERVENTIONAL
Allocation
NON_RANDOMIZED
Purpose
TREATMENT
Masking
NONE
Enrollment
233
6mg/kg/week
Differences between the 6MWD at baseline and Week 104
Time frame: 104 weeks
Timed Function tests
Time frame: 104 weeks
Muscle strength
Time frame: 104 weeks
North Star Ambulatory Assessment Scores
Time frame: 104 weeks
Creatine kinase Serum concentrations
Time frame: 104 weeks
Pulmonary Function
Time frame: 104 weeks
Pediatric Quality of Life Neuromuscular module
Time frame: 104weeks
Clinician Global Impression of Improvement
Time frame: 104 weeks
Health Utilities Index
Time frame: 104 weeks
Frequency of accidental falls during 6 Minute Walk Distance test
Time frame: 104 weeks
Functional Outcomes Assessment
Time frame: 104 weeks
Time to major disease milestones
Time frame: 104 weeks
This platform is for informational purposes only and does not constitute medical advice. Always consult a qualified healthcare professional.
GSK Investigational Site
Ciudad Autónoma de Buenos Aires, Buenos Aires, Argentina
GSK Investigational Site
Westmead, New South Wales, Australia
GSK Investigational Site
Parkville, Victoria, Australia
GSK Investigational Site
Ghent, Belgium
GSK Investigational Site
Leuven, Belgium
GSK Investigational Site
Curitiba, Paraná, Brazil
GSK Investigational Site
Rio de Janeiro, Rio de Janeiro, Brazil
GSK Investigational Site
Porto Alegre, Rio Grande do Sul, Brazil
GSK Investigational Site
Ribeirão Preto, São Paulo, Brazil
GSK Investigational Site
Santo André, São Paulo, Brazil
...and 49 more locations