The purpose of this study is: * To evaluate whether 7-day treatment with oral QLT091001 can improve visual function in RP subjects with an autosomal dominant mutation in RPE65. * To evaluate duration of visual function improvement (if observed) in RP subjects with an autosomal dominant mutation in RPE65 after 7-day treatment with oral QLT091001. * To evaluate the safety of oral QLT091001 administered once daily for 7 days in RP subjects with an autosomal dominant mutation in RPE65.
Study Type
INTERVENTIONAL
Allocation
NA
Purpose
TREATMENT
Masking
NONE
Enrollment
5
oral QLT091001 administered once daily for 7 days
Montreal Children's Hospital, McGill University Health Centre
Montreal, Quebec, Canada
Royal Victoria Eye and Ear Hospital
Dublin, Ireland
Visual field
Time frame: 12 months
Safety will be assessed by evaluating the following: adverse events, clinical laboratory results, ECG's and vital signs
Time frame: 12 months
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