A Long-term Study for the Outcome of Pompe Disease

N/ARecruitingNCT02399748

National Taiwan University Hospital50 enrolled

Overview

Prospectively follow patients with Pompe disease underwent enzyme replacement therapy.

Study Type

OBSERVATIONAL

Enrollment

Sex: ALL

Medical Language ↔ Plain English

Inclusion Criteria: Confirm diagnosis with Pompe disease, is or is preparing receiving enzyme replacement therapy Exclusion Criteria: No

National Taiwan University Hospital

Taipei, Taiwan

RECRUITING

all cause morbidities

Time frame: 10 years

Yin-Hsiu Chien

CONTACT

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