This study will evaluate the safety of tisagenlecleucel that is out of specification( OOS) for release as commercial product. Specifically, this study will evaluate the safety of CTL019 in the patients treated within the approved label by Japan Health Authority in Part 2. Only for Part 1, in addition to safety, key efficacy of CTL019 will also be evaluated.
This is a single-arm, open-label, multicenter, interventional Phase IIIb study in pediatric/young adult patients with relapsed/refractory (r/r) B-cell acute lymphoblastic leukemia (pALL) and adult patients with r/r large B-cell lymphoma (LBCL) including diffuse large B-cell lymphoma (DLBCL) not otherwise specified, high-grade B cell lymphoma, and DLBCL arising from follicular lymphoma for Part 1 and and r/r ALL and r/r non-Hodgkin's lymphomas (NHL) for Part 2 Patients whose final manufactured tisagenlecleucel patient-specific batch does not meet the approved local commercial release specifications are eligible for inclusion. Each case will be individually assessed and approved by the Novartis manufacturing facility and the Novartis global medical team (including Patient Safety). Following a single infusion of CTL019, the patient will be followed for 3 months for Part 1, and 1 day for Part 2.
Study Type
INTERVENTIONAL
Allocation
NA
Purpose
TREATMENT
Masking
NONE
Enrollment
200
A single intravenous (i.v.) infusion of CAR-positive viable T cells.
Percentage of participants with Adverse Events (AEs)
Percentage of participants with Serious AEs (SAEs) and non-SAEs
Time frame: From Screening up to 3 months for Part 1 and 1 day for Part 2
Part 1: Overall Remission Rate in Group A (pALL)
Overall Remission Rate is defined as the percentage of participants wiho achieve a complete remission (CR) and CR with incomplete blood count recovery (CRi) within 3 months following infusion of CTL019 as determined by the local investigator assessment for participants in group A (part 1).
Time frame: Up to 3 months
Part 1: Overall Response Rate in Group B (LBCL)
ORR is defined as the percentage of patients who achieve a domplete response and partial response within 3 months following infusion of CTL019 as determined by the local investigator assessment for participants in group B (part 1).
Time frame: Up to 3 months
This platform is for informational purposes only and does not constitute medical advice. Always consult a qualified healthcare professional.
Novartis Investigative Site
Hamilton, Ontario, Canada
COMPLETEDNovartis Investigative Site
Ottawa, Ontario, Canada
WITHDRAWNNovartis Investigative Site
Toronto, Ontario, Canada
COMPLETEDNovartis Investigative Site
Toronto, Ontario, Canada
COMPLETEDNovartis Investigative Site
Montreal, Quebec, Canada
WITHDRAWNNovartis Investigative Site
Québec, Quebec, Canada
WITHDRAWNNovartis Investigative Site
Nagoya, Aichi-ken, Japan
RECRUITINGNovartis Investigative Site
Nagoya, Aichi-ken, Japan
RECRUITINGNovartis Investigative Site
Tōon, Ehime, Japan
RECRUITINGNovartis Investigative Site
Gifu, Gifu, Japan
RECRUITING...and 45 more locations