The compassionate use programme will give participants concizumab for free, even though it is not yet approved by health authorities. This is because participants need this medicine to treat their haemophilia properly. The programme will check that participants are safe and that the medicine works for them. The programme may last for years. Participants will take one injection under their skin every day. Participants will have 4-5 visits with the study doctor for the first half year. After that they will have 1 visit every half year. At all clinic visits participants will have blood samples taken. Participants will fill in a diary between the visits. A patient is considered to have completed the programme when any of the following criteria occurred first: 1) when the patient is included in a clinical trial with concizumab or 2) up to 6 months after concizumab is commercially available in the patient's country and approved for the patient (The time span of 6 months should provide ample time for the patient to obtain concizumab commercially) or 3) the sponsor decides to discontinue concizumab clinical development for the patient's population.
Study Type
EXPANDED_ACCESS
Injected under the skin (subcutaneous, sc) once daily, individual dose adjustment.
Children's Hospital Los Angeles - Endocrinology
Los Angeles, California, United States
AVAILABLEUniversity of California San Francisco UCSF
San Francisco, California, United States
AVAILABLEConnecticut Children's Medical Center
Hartford, Connecticut, United States
AVAILABLEGeorgetown University Medical Center
Washington D.C., District of Columbia, United States
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Augusta University
Augusta, Georgia, United States
AVAILABLEMemorial Health University Medical Center
Savannah, Georgia, United States
AVAILABLESt. Luke's Mountain States Tumor Institute
Boise, Idaho, United States
AVAILABLEChildrens Hospital of Chicago
Chicago, Illinois, United States
AVAILABLEIndiana Hemophilia-Thromb Ctr
Indianapolis, Indiana, United States
AVAILABLEChildren's Hosp-New Orleans
New Orleans, Louisiana, United States
AVAILABLE...and 15 more locations