The objective of this study is to collect information on patients with cardiomyopathy (CM) due to mutations in the MYBPC3 gene, to evaluate their disease course, burden of illness, risk factors for this disease, and the quality of life (QoL). This study will also collect information on treatments, procedures and outcome in infants and children up to 18 yrs who have this mutation.
Study Type
OBSERVATIONAL
Enrollment
200
To characterize the disease course and natural history in participants with pathogenic or likely pathogenic MYBPC3 mutations with a specific focus on cardiac events and measurement
Time frame: 5 years for prospective group, n/a for retrospective group
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Arkansas Children's Hospital
Little Rock, Arkansas, United States
RECRUITINGChildren's Hospital Los Angeles
Los Angeles, California, United States
RECRUITINGUniversity of California Davis Health
Sacramento, California, United States
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San Diego, California, United States
RECRUITINGUniversity of Colorado Hospital - Anschutz Medical Campus
Aurora, Colorado, United States
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Kansas City, Missouri, United States
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St Louis, Missouri, United States
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Lake Success, New York, United States
RECRUITING...and 19 more locations