This is an observational screening study to evaluate the prevalence of anti-adeno-associated serotype 8 (AAV8) antibodies in participants with Duchenne muscular dystrophy (DMD).
This is an observational screening study to evaluate the prevalence of anti-adeno-associated serotype 8 (AAV8) antibodies in participants with Duchenne muscular dystrophy (DMD). Information collected in this study may be used to identify potential participants for DMD investigational gene therapy clinical trials. This study consists of: * A phone/video interview or at an in-clinic visit to provide e-consent and medical history * A single home health visit or subsequent in-clinic visit to collect blood sample for antibody testing * A phone/video call for communication of AAV8 antibody test results
Study Type
OBSERVATIONAL
Enrollment
200
An in vitro diagnostic assay to detect antibodies to AAV8 in human serum specimens.
Rare Disease Research
Atlanta, Georgia, United States
Prevalence of anti-AAV8 antibodies in patients with DMD
* To evaluate the prevalence of AAV8 antibodies in patients with DMD * To identify participants who may be eligible for investigational gene therapy clinical trials in males with DMD
Time frame: 90 days
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