The goal of this open label study is to measure pharmacokinetics, pharmacodynamics, early efficacy, and safety of tanruprubart in adult and pediatric participants, in the United States, Canada, and Europe.
Study Type
INTERVENTIONAL
Allocation
NA
Purpose
TREATMENT
Masking
NONE
Enrollment
30
Solution for IV infusion.
St. Joseph's Hospital & Medical Center - Barrow Neurological Institute
Phoenix, Arizona, United States
RECRUITINGHonorHealth Bob Bové Neuroscience Institute
Scottsdale, Arizona, United States
Area Under the Tanruprubart Serum Concentration-time Curve to the Last Sample (AUC0-t)
Time frame: Up to Day 15
Observed Time to Maximum Observed Serum Concentration (Cmax) (Tmax) of Tanruprubart
Time frame: Up to Day 15
Change From Baseline in Free Component of Complement Complex (C1q) Protein Concentration in Serum
Time frame: Baseline up to Day 15
Change from Baseline in Medical Research Council (MRC) Sumscore at Week 1
Time frame: Baseline, Week 1
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Profound Research LLC
Carlsbad, California, United States
RECRUITINGChildren's Hospital of Orange County
Orange, California, United States
RECRUITINGUniversity of California Irvine
Orange, California, United States
RECRUITINGUniversity of Colorado Hospital
Aurora, Colorado, United States
RECRUITINGMayo Clinic Florida
Jacksonville, Florida, United States
RECRUITINGUniversity of Kansas Medical Center
Kansas City, Kansas, United States
RECRUITINGOchsner LSU Health
Shreveport, Louisiana, United States
RECRUITINGUniversity Massachusetts Chan Medical School
Worcester, Massachusetts, United States
RECRUITING...and 3 more locations