The purpose of this study is to learn about the long-term safety and tolerability of PGN-EDODM1 in participants with myotonic dystrophy type 1 (DM1) who have completed a prior study with PGN-EDODM1.
Study Type
INTERVENTIONAL
Allocation
NA
Purpose
TREATMENT
Masking
NONE
Enrollment
48
Administered by intravenous (IV) infusion
University of Calgary
Calgary, Alberta, Canada
RECRUITINGOttawa Hospital Research Institute
Ottawa, Ontario, Canada
RECRUITINGCIUSSS du Saguenay-Lac-Saint-Jean
Saguenay, Canada
RECRUITINGSafety and tolerability as assessed by number of participants with Adverse Events (AEs)
Time frame: Baseline through Week 108
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