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Results for “β Thalassemia Major”

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Showing 20 of 0 results

Testing effectiveness (Phase 2)Not Yet RecruitingNCT07489196
What this trial is testing

Safety and Efficacy Study Evaluating CS-101 in Participants With β-Thalassemia Major

Who this might be right for
β-thalassemia Major
CorrectSequence Therapeutics Co., Ltd 20
Testing effectiveness (Phase 2)Study completedNCT01745120
What this trial is testing

A Study Evaluating the Safety and Efficacy of the LentiGlobin BB305 Drug Product in β-Thalassemia Major Participants

Who this might be right for
β-thalassemia Major
Genetix Biotherapeutics Inc. 19
Large-scale testing (Phase 3)Study completedNCT06146478
What this trial is testing

Deciphering Effects of Thalidomide on Red Blood Cells in Transfusion Dependents Beta Thalassemia Patients

Who this might be right for
Transfusion-dependent Beta-Thalassemia
Blood Care Clinic 200
Not applicableLooking for participantsNCT06073860
What this trial is testing

A Post-Marketing Surveillance Study to Assess Safety of Luspatercept in Korean Patients With Myelodysplastic Syndrome or β-thalassemia

Who this might be right for
Myelodysplastic SyndromeBeta Thalassemia
Bristol-Myers Squibb 104
Testing effectiveness (Phase 2)Study completedNCT00809042
What this trial is testing

Combination Therapy of Hydroxyurea With L-Carnitine and Magnesium Chloride in Thalassemia Intermedia

Who this might be right for
β-Thalassemia Intermedia
Shiraz University of Medical Sciences 120
Early research (Phase 1)Active Not RecruitingNCT01639690
What this trial is testing

SS-Thalassemia Major With Autologous CD34+ Hematopoietic Progenitor Cells Transduced With TNS9.3.55 a Lentiviral Vector Encoding the Normal Human ß-Globin Gene

Who this might be right for
Confirmed Diagnosis of ß-thalassemia Major
San Rocco Therapeutics 10
Not applicableLooking for participantsNCT05776173
What this trial is testing

Safety and Efficacy of Gene Modified Autologous Hematopoietic Stem Cells to Treat Transfusion-dependent β-thalassemia

Who this might be right for
β-thalassemia Major
Shanghai BDgene Co., Ltd. 10
Not applicableActive Not RecruitingNCT02633943
What this trial is testing

Long-term Follow-up of Subjects With Transfusion-Dependent β-Thalassemia (TDT) Treated With Ex Vivo Gene Therapy

Who this might be right for
Transfusion-dependent Beta-Thalassemia
Genetix Biotherapeutics Inc. 66
Testing effectiveness (Phase 2)Study completedNCT04364269
What this trial is testing

Safety, Tolerability, Pharmacokinetics (PK), Pharmacodynamics (PD) and Preliminary Efficacy of VIT-2763 in β-thalassaemia

Who this might be right for
Beta-ThalassemiaNon-transfusion-dependent Thalassemia
Vifor (International) Inc. 35
Post-approval studies (Phase 4)UnknownNCT01846923
What this trial is testing

B Memory Cell Response to Vaccination With the 13-valent Pneumococcal Conjugate Vaccine in Asplenic Individuals

Who this might be right for
Aspleniaβ-thalassemia Major
Aghia Sophia Children's Hospital of Athens 37
Large-scale testing (Phase 3)Active Not RecruitingNCT05356195
What this trial is testing

Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Transfusion-Dependent β-Thalassemia (TDT)

Who this might be right for
Beta-ThalassemiaThalassemiaGenetic Diseases, Inborn+2 more
Vertex Pharmaceuticals Incorporated 16
Testing effectiveness (Phase 2)Ended earlyNCT01571635
What this trial is testing

Study to Determine the Safety and Tolerability of Sotatercept (ACE-011) in Adults With Beta( β)- Thalassemia.

Who this might be right for
Beta Thalassemia MajorBeta Thalassemia Intermedia
Celgene 46
Not applicableLooking for participantsNCT06219239
What this trial is testing

Safety and Efficacy of the Lentiviral Vector in Gene Therapy of Beta-thalassemia Patients

Who this might be right for
Transfusion-dependent Beta-Thalassemia
Institute of Hematology & Blood Diseases Hospital, China 3
Very early researchLooking for participantsNCT05762510
What this trial is testing

A Study Evaluating the Safety and Efficacy of LentiRed Drug Product in Transfusion-dependent β-Thalassemia [TDT]

Who this might be right for
Transfusion Dependent Beta-Thalassemia
First Affiliated Hospital of Guangxi Medical University 5
Not applicableUnknownNCT03822585
What this trial is testing

Detection Of β-thalassemia Carriers In Assiut

Who this might be right for
Beta-Thalassemia
Assiut University 100
Testing effectiveness (Phase 2)Not Yet RecruitingNCT07721480
What this trial is testing

Gene Therapy for Patients With Transfusion-Dependent β-Thalassemia

Who this might be right for
Beta Thalassemia Transfusion Dependent
Prince of Wales Hospital, Shatin, Hong Kong 6
Not applicableStudy completedNCT02626689
What this trial is testing

To Document the Burden of Illness on the Quality of Life and the Impact on Healthcare Utilization in (Beta) β-thalassemia Subjects Who Are Transfusion Dependent (TD) and Non-transfusion Dependent (NTD) Receiving Standard of Care

Who this might be right for
Beta-Thalassemia
Celgene 100
Not applicableNot Yet RecruitingNCT07614217
What this trial is testing

Oral Health Status in Children With β-Thalassemia Major

Who this might be right for
B Thalassemia Major
Cairo University 45
Not applicableStudy completedNCT04390971
What this trial is testing

Safety and Efficacy Evaluation of ET-01 Transplantation in Subjects With Transfusion Dependent β-Thalassaemia

Who this might be right for
Transfusion Dependent Beta-Thalassaemia
Institute of Hematology & Blood Diseases Hospital, China 3
Testing effectiveness (Phase 2)Ended earlyNCT04059406
What this trial is testing

Study to Evaluate the Efficacy, Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Sapablursen (Formerly ISIS 702843, IONIS-TMPRSS6-LRx)

Who this might be right for
Beta Thalassemia Intermedia
Ionis Pharmaceuticals, Inc. 29
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