Not applicableUnknownNCT05133388What this trial is testingThe Prevelence of HBB c.93-21 G-A in β Thalassemia PatientsWho this might be right forBeta-Thalassemia Assiut University 150
Testing effectiveness (Phase 2)Study completedNCT00809042What this trial is testingCombination Therapy of Hydroxyurea With L-Carnitine and Magnesium Chloride in Thalassemia IntermediaWho this might be right forβ-Thalassemia Intermedia Shiraz University of Medical Sciences 120
Not applicableEnrolling By InvitationNCT06685536What this trial is testingA Long-term Follow-up Study in Participants Who Received CS-101Who this might be right forBeta-Thalassemia CorrectSequence Therapeutics Co., Ltd 5
Not applicableLooking for participantsNCT06219239What this trial is testingSafety and Efficacy of the Lentiviral Vector in Gene Therapy of Beta-thalassemia PatientsWho this might be right forTransfusion-dependent Beta-Thalassemia Institute of Hematology & Blood Diseases Hospital, China 3
Not applicableLooking for participantsNCT06271512What this trial is testingParticipants with Β-Thalassemia Treated with Betibeglogene AutotemcelWho this might be right forBeta-Thalassemia Genetix Biotherapeutics Inc. 150
Early research (Phase 1)Study completedNCT06291961What this trial is testingA Safety and Efficacy Study Evaluating CS-101 in Subjects With β-Thalassemia MajorWho this might be right forBeta-Thalassemia Major CorrectSequence Therapeutics Co., Ltd 9
Not applicableStudy completedNCT06468423What this trial is testingComparison of Deferasirox and Desferoxamine in Patients of β-Thalassemia Major With Iron OverloadWho this might be right forPateints of β-thalassemia Major With Iron Overload RESnTEC, Institute of Research 142
Testing effectiveness (Phase 2)Study completedNCT00390858What this trial is testingA 4-year Extension Study to Core 1-year Study of Iron Chelation Therapy With Deferasirox in β-thalassemia Major Pediatric Patients With Transfusional Iron Overload.Who this might be right forTransfusional Iron Overloadβ-thalassemia MajorPediatric Rare Anemia Novartis Pharmaceuticals 40
Testing effectiveness (Phase 2)Active Not RecruitingNCT05567458What this trial is testingEvaluate Luspatercept (ACE-536) in Chinese Participants Who Require Regular Red Blood Cell Transfusions Due to Beta (β)-Thalassemia.Who this might be right forBeta-thalassemia Bristol-Myers Squibb 94
Not applicableLooking for participantsNCT05773729What this trial is testingSafety and Efficacy of Gene Modified Autologous Hematopoietic Stem Cells to Treat Transfusion-dependent Beta-thalassemiaWho this might be right forβ-thalassemia Shanghai BDgene Co., Ltd. 10
Not applicableLooking for participantsNCT06314529What this trial is testingLong-term Follow-up Study of BHC001 for TDTWho this might be right forThalassemia, Beta Bioray Laboratories 6
Testing effectiveness (Phase 2)Not Yet RecruitingNCT07721480What this trial is testingGene Therapy for Patients With Transfusion-Dependent β-ThalassemiaWho this might be right forBeta Thalassemia Transfusion Dependent Prince of Wales Hospital, Shatin, Hong Kong 6
Early research (Phase 1)Ended earlyNCT02274233What this trial is testingSafety and Pharmacokinetic Study of Escalating Doses of SP-420, an Iron Chelator, in Patients With β-ThalassemiaWho this might be right forIron OverloadBeta-Thalassemia Sideris Pharmaceuticals 24
Very early researchStudy completedNCT06065189What this trial is testingBase-edited Autologous Hematopoietic Stem Cell Transplantation in Treating Patients With β-thalassemia MajorWho this might be right forBeta-Thalassemia Children's Hospital of Fudan University 2
Testing effectiveness (Phase 2)Study completedNCT07292259What this trial is testingCombination of Thalidomide and Hydroxyuria in Transfusion Dependent ThalasemmiaWho this might be right forTransfusion Dependent Beta Thalassemia Pakistan Blood and Marrow Transplant (PBMT) Group 100
Testing effectiveness (Phase 2)Ended earlyNCT04059406What this trial is testingStudy to Evaluate the Efficacy, Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Sapablursen (Formerly ISIS 702843, IONIS-TMPRSS6-LRx)Who this might be right forBeta Thalassemia Intermedia Ionis Pharmaceuticals, Inc. 29
Very early researchLooking for participantsNCT05745532What this trial is testingSafety and Efficacy Evaluation of β-globin Restored Autologous Hematopoietic Stem Cells in β-thalassemia Major PatientsWho this might be right forβ-thalassemia Shenzhen Hemogen 10
Not applicableLooking for participantsNCT05776173What this trial is testingSafety and Efficacy of Gene Modified Autologous Hematopoietic Stem Cells to Treat Transfusion-dependent β-thalassemiaWho this might be right forβ-thalassemia Major Shanghai BDgene Co., Ltd. 10
Testing effectiveness (Phase 2)Study completedNCT02151526What this trial is testingA Study Evaluating the Safety and Efficacy of LentiGlobin BB305 Drug Product in β-Thalassemia Major (Also Referred to as Transfusion-dependent β-Thalassemia [TDT]) and Sickle Cell DiseaseWho this might be right forBeta-Thalassemia MajorSickle Cell Disease Genetix Biotherapeutics Inc. 7
Not applicableLooking for participantsNCT06734520What this trial is testingClinical Study of Super Transplantation in the Treatment of Severe β-thalassemiaWho this might be right forThalassemia Majors (Beta-Thalassemia Major)Haplo-identical Donors Guangzhou Women and Children's Medical Center 3