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Results for “β-Thalassemia Major”

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Showing 20 of 0 results

Testing effectiveness (Phase 2)Study completedNCT01745120
What this trial is testing

A Study Evaluating the Safety and Efficacy of the LentiGlobin BB305 Drug Product in β-Thalassemia Major Participants

Who this might be right for
β-thalassemia Major
Genetix Biotherapeutics Inc. 19
Large-scale testing (Phase 3)Active Not RecruitingNCT04770779
What this trial is testing

A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)

Who this might be right for
Transfusion-dependent Alpha-ThalassemiaTransfusion-dependent Beta-Thalassemia
Agios Pharmaceuticals, Inc. 258
Post-approval studies (Phase 4)UnknownNCT01846923
What this trial is testing

B Memory Cell Response to Vaccination With the 13-valent Pneumococcal Conjugate Vaccine in Asplenic Individuals

Who this might be right for
Aspleniaβ-thalassemia Major
Aghia Sophia Children's Hospital of Athens 37
Testing effectiveness (Phase 2)Looking for participantsNCT04143724
What this trial is testing

Study of Safety & PK of Luspatercept (ACE-536) in Pediatric Participants With Beta (β)-Thalassemia

Who this might be right for
Beta-Thalassemia
Celgene 99
Not applicableUnknownNCT03822585
What this trial is testing

Detection Of β-thalassemia Carriers In Assiut

Who this might be right for
Beta-Thalassemia
Assiut University 100
Not applicableStudy completedNCT02626689
What this trial is testing

To Document the Burden of Illness on the Quality of Life and the Impact on Healthcare Utilization in (Beta) β-thalassemia Subjects Who Are Transfusion Dependent (TD) and Non-transfusion Dependent (NTD) Receiving Standard of Care

Who this might be right for
Beta-Thalassemia
Celgene 100
Large-scale testing (Phase 3)Looking for participantsNCT07517133
What this trial is testing

Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With α- or β-Non-Transfusion-Dependent Thalassemia

Who this might be right for
Non-Transfusion-dependent Alpha-ThalassemiaNon-Transfusion-dependent Beta-Thalassemia
Agios Pharmaceuticals, Inc. 45
Early research (Phase 1)Ended earlyNCT02274233
What this trial is testing

Safety and Pharmacokinetic Study of Escalating Doses of SP-420, an Iron Chelator, in Patients With β-Thalassemia

Who this might be right for
Iron OverloadBeta-Thalassemia
Sideris Pharmaceuticals 24
Testing effectiveness (Phase 2)Active Not RecruitingNCT05577312
What this trial is testing

Safety and Efficacy Evaluation of BRL-101 in Subjects With Transfusion-Dependent β-Thalassemia

Who this might be right for
Beta-Thalassemia
Bioray Laboratories 39
Testing effectiveness (Phase 2)Looking for participantsNCT05736419
What this trial is testing

Immune Suppression Treatment for People With Sickle Cell Disease or β-Thalassemia Who Are Going to Receive an Allogeneic Hematopoietic Cell Transplantation (HCT)

Who this might be right for
Sickle Cell DiseaseThalassemia, BetaThalassemia
Memorial Sloan Kettering Cancer Center 24
Not applicableStudy completedNCT06468423
What this trial is testing

Comparison of Deferasirox and Desferoxamine in Patients of β-Thalassemia Major With Iron Overload

Who this might be right for
Pateints of β-thalassemia Major With Iron Overload
RESnTEC, Institute of Research 142
Testing effectiveness (Phase 2)Not Yet RecruitingNCT07721480
What this trial is testing

Gene Therapy for Patients With Transfusion-Dependent β-Thalassemia

Who this might be right for
Beta Thalassemia Transfusion Dependent
Prince of Wales Hospital, Shatin, Hong Kong 6
Not applicableNot Yet RecruitingNCT07614217
What this trial is testing

Oral Health Status in Children With β-Thalassemia Major

Who this might be right for
B Thalassemia Major
Cairo University 45
Very early researchLooking for participantsNCT05762510
What this trial is testing

A Study Evaluating the Safety and Efficacy of LentiRed Drug Product in Transfusion-dependent β-Thalassemia [TDT]

Who this might be right for
Transfusion Dependent Beta-Thalassemia
First Affiliated Hospital of Guangxi Medical University 5
Not applicableStudy completedNCT04211480
What this trial is testing

Safety and Efficacy Evaluation of γ-globin Reactivated Autologous Hematopoietic Stem Cells

Who this might be right for
β Thalassemia Major
Bioray Laboratories 6
Not applicableLooking for participantsNCT05776173
What this trial is testing

Safety and Efficacy of Gene Modified Autologous Hematopoietic Stem Cells to Treat Transfusion-dependent β-thalassemia

Who this might be right for
β-thalassemia Major
Shanghai BDgene Co., Ltd. 10
Early research (Phase 1)Looking for participantsNCT06647979
What this trial is testing

Hematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies

Who this might be right for
Sickle Cell DiseaseSickle Cell Anemia (HbSS, or HbSβ-thalassemia0)Beta-Thalassemia+1 more
Daniel Bauer 10
Testing effectiveness (Phase 2)Study completedNCT03802201
What this trial is testing

Study of PTG-300 in Non-Transfusion Dependent and Transfusion-Dependent Beta-Thalassemia Subjects With Chronic Anemia

Who this might be right for
β-thalassemiaIneffective ErythropoiesisChronic Anemia
Protagonist Therapeutics, Inc. 63
Not applicableLooking for participantsNCT07207577
What this trial is testing

Evaluation of Physiological and Psychological Factors Involved in Exercise Intolerance in Patients With β-TTD

Who this might be right for
Beta Thalassemia Transfusion Dependent
Centre Hospitalier Metropole Savoie 36
Testing effectiveness (Phase 2)Study completedNCT02151526
What this trial is testing

A Study Evaluating the Safety and Efficacy of LentiGlobin BB305 Drug Product in β-Thalassemia Major (Also Referred to as Transfusion-dependent β-Thalassemia [TDT]) and Sickle Cell Disease

Who this might be right for
Beta-Thalassemia MajorSickle Cell Disease
Genetix Biotherapeutics Inc. 7
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