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Results for “β-thalassemia”

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Showing 20 of 0 results

Not applicableActive Not RecruitingNCT06596642
What this trial is testing

A Real-World Study of β-Thalassemia Major Treatment With Luspatercept in Taiwan

Who this might be right for
β-Thalassemia Major
Bristol-Myers Squibb 61
Testing effectiveness (Phase 2)Ended earlyNCT00586209
What this trial is testing

L-Glutamine Therapy for Sickle Cell Anemia

Who this might be right for
Sickle Cell AnemiaThalassemia
Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center 15
Not applicableNot Yet RecruitingNCT05883254
What this trial is testing

Pumilio1 (PUM1) Expression, Sickle Cell Anemia, β-thalassemia Intermedia

Who this might be right for
Sickle Cell Disease, Beta Thalassemia Intermedia
Assiut University 80
Not applicableStudy completedNCT02307786
What this trial is testing

Long Term Outcomes in β Thalassemia Major

Who this might be right for
Thalassemia Major
Ann & Robert H Lurie Children's Hospital of Chicago 176
Large-scale testing (Phase 3)Looking for participantsNCT07506863
What this trial is testing

Investigate the Efficacy, Pharmacokinetics, and Safety of Mitapivat in Pediatric Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)

Who this might be right for
Transfusion-dependent Alpha-ThalassemiaTransfusion-dependent Beta-Thalassemia
Agios Pharmaceuticals, Inc. 54
Testing effectiveness (Phase 2)Study completedNCT01044186
What this trial is testing

A Protocol to Allow Treatment With ICL670 for Patients With or at Risk of Life-threatening Complications of Transfusional Iron Overload Who Are Unable to Tolerate Other Iron Chelators Because of Documented Severe Toxicity

Who this might be right for
Transfusional Iron Overload
Novartis Pharmaceuticals 30
Large-scale testing (Phase 3)Looking for participantsNCT05477563
What this trial is testing

Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease

Who this might be right for
Beta-ThalassemiaThalassemiaHematologic Diseases+4 more
Vertex Pharmaceuticals Incorporated 26
Testing effectiveness (Phase 2)Active Not RecruitingNCT06421636
What this trial is testing

Test the Safety, Tolerability, and Efficacy of an Antibody, REGN7999, Injected Under the Skin for the Treatment of Iron Overload in Adult Participants With Non-Transfusion Dependent β-thalassemia, Using MRI Scans to Measure Iron Levels in the Body

Who this might be right for
Non-Transfusion Dependent Beta-Thalassemia (NTDT)
Regeneron Pharmaceuticals 19
Not applicableEnrolling By InvitationNCT06685536
What this trial is testing

A Long-term Follow-up Study in Participants Who Received CS-101

Who this might be right for
Beta-Thalassemia
CorrectSequence Therapeutics Co., Ltd 5
Testing effectiveness (Phase 2)Study completedNCT00390858
What this trial is testing

A 4-year Extension Study to Core 1-year Study of Iron Chelation Therapy With Deferasirox in β-thalassemia Major Pediatric Patients With Transfusional Iron Overload.

Who this might be right for
Transfusional Iron Overloadβ-thalassemia MajorPediatric Rare Anemia
Novartis Pharmaceuticals 40
Early research (Phase 1)Looking for participantsNCT06655662
What this trial is testing

Evaluating Safety and Efficacy of Lentiviral-transduced CD34+ HSCs in Β-thalassaemia Patients.

Who this might be right for
Β-thalassemia
Shenzhen Hemogen 8
Testing effectiveness (Phase 2)Ended earlyNCT01571635
What this trial is testing

Study to Determine the Safety and Tolerability of Sotatercept (ACE-011) in Adults With Beta( β)- Thalassemia.

Who this might be right for
Beta Thalassemia MajorBeta Thalassemia Intermedia
Celgene 46
Early research (Phase 1)Ended earlyNCT04925206
What this trial is testing

A Safety and Efficacy Study Evaluating ET-01 in Subjects with Transfusion Dependent Β-Thalassaemia

Who this might be right for
Transfusion Dependent Beta-Thalassaemia
EdiGene (GuangZhou) Inc. 8
Very early researchUnknownNCT03728322
What this trial is testing

IHSCs With the Gene Correction of HBB Intervent Subjests With β-thalassemia Mutations

Who this might be right for
Thalassemia
Allife Medical Science and Technology Co., Ltd. 12
Large-scale testing (Phase 3)Study completedNCT02906202
What this trial is testing

A Study Evaluating the Efficacy and Safety of the LentiGlobin® BB305 Drug Product in Participants With Transfusion-Dependent β-Thalassemia, Who do Not Have a β0/β0 Genotype

Who this might be right for
Beta-Thalassemia
Genetix Biotherapeutics Inc. 24
Testing effectiveness (Phase 2)Study completedNCT02268409
What this trial is testing

Extension Study to Evaluate the Safety and Efficacy of Luspatercept in Participants With β-Thalassemia Previously Enrolled in A536-04 (A536-06/MK-6143-004)

Who this might be right for
β-Thalassemia
Acceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway, NJ USA 51
Early research (Phase 1)Looking for participantsNCT06465550
What this trial is testing

Gene-modified Autologous Hematopoietic Stem Cell (BD211) Treating β-thalassemia Major

Who this might be right for
β-thalassemia
Shanghai BDgene Co., Ltd. 9
Not applicableStudy completedNCT05506358
What this trial is testing

Evaluation of Low-cost Techniques for Detecting Sickle Cell Disease and β-thalassemia in Nepal and Canada

Who this might be right for
Sickle Cell DiseaseSickle Cell TraitBeta-Thalassemia+2 more
University of British Columbia 145
Large-scale testing (Phase 3)Study completedNCT06146478
What this trial is testing

Deciphering Effects of Thalidomide on Red Blood Cells in Transfusion Dependents Beta Thalassemia Patients

Who this might be right for
Transfusion-dependent Beta-Thalassemia
Blood Care Clinic 200
Testing effectiveness (Phase 2)Study completedNCT04054921
What this trial is testing

Safety Study for Beta Thalassemia Subjects on PTG-300

Who this might be right for
β-thalassemiaIneffective Erythropoiesis
Protagonist Therapeutics, Inc. 34
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