Not applicableUnknownNCT05133388What this trial is testingThe Prevelence of HBB c.93-21 G-A in β Thalassemia PatientsWho this might be right forBeta-Thalassemia Assiut University 150
Not applicableStudy completedNCT00159029What this trial is testingGenetics of Alpha Thalassemia in Israeli Ethnic GroupsWho this might be right forAlpha Thalassemia Deborah Rund 100
Post-approval studies (Phase 4)Study completedNCT00707850What this trial is testingPegasys® Plus Ribavirin in Thalassemic Patients With Hepatitis C Virus InfectionWho this might be right forHepatitis CThalassemia Baqiyatallah Medical Sciences University 300
Not applicableActive Not RecruitingNCT02692872What this trial is testingScreening for Alpha Thalassemia in Healthy VolunteersWho this might be right forAlpha Thalassemia National Institute of Allergy and Infectious Diseases (NIAID) 367
Testing effectiveness (Phase 2)WithdrawnNCT04938635What this trial is testingEfficacy and Safety Study of Multiple Doses of VIT-2763 in Adults With Transfusion-dependent Beta-thalassemiaWho this might be right forBeta-Thalassemia Vifor (International) Inc.
Not applicableStudy completedNCT04973280What this trial is testingStudy to Evaluate Additional Risk Minimisation Measures (aRMMs) for REBLOZYL Among Healthcare Professionals (HCPs)Who this might be right forMyelodysplastic SyndromesBeta-thalassemia Celgene 187
Not applicableEnrolling By InvitationNCT06685536What this trial is testingA Long-term Follow-up Study in Participants Who Received CS-101Who this might be right forBeta-Thalassemia CorrectSequence Therapeutics Co., Ltd 5
Testing effectiveness (Phase 2)WithdrawnNCT01419704What this trial is testingPhase I/II Pilot Study of Mixed Chimerism to Treat HemoglobinopathiesWho this might be right forAnemia, Sickle CellComplex and Transfusion-dependent HemoglobinopathiesThalassemia+4 more Talaris Therapeutics Inc.
Early research (Phase 1)Study completedNCT03492931What this trial is testingPK Study of Ticagrelor in Children Aged Less Than 24 Months, With Sickle Cell Disease (HESTIA4)Who this might be right forSickle Cell Disease AstraZeneca 21
Not applicableLooking for participantsNCT06271512What this trial is testingParticipants with Β-Thalassemia Treated with Betibeglogene AutotemcelWho this might be right forBeta-Thalassemia Genetix Biotherapeutics Inc. 150
Early research (Phase 1)Study completedNCT06291961What this trial is testingA Safety and Efficacy Study Evaluating CS-101 in Subjects With β-Thalassemia MajorWho this might be right forBeta-Thalassemia Major CorrectSequence Therapeutics Co., Ltd 9
Early research (Phase 1)Study completedNCT06813924What this trial is testingA Research Study of the Effect of Etavopivat on Other Drugs in Healthy ParticipantsWho this might be right forHealthy Volunteers Sickle Cell Disease, Thalassemia Novo Nordisk A/S 37
Not applicableUnknownNCT01935661What this trial is testingA Case Control Study to Evaluate the Cognitive and Brain Function of β-thalassemia Patients.Who this might be right forThalassemiaBrain Function (Measured by ERP Level) HaEmek Medical Center, Israel 120
Early research (Phase 1)Study completedNCT03673085What this trial is testingClinical Study of CN128 in Thalassemia PatientsWho this might be right forThalassemia Hangzhou Zede Pharma-Tech Co., Ltd. 32
Testing effectiveness (Phase 2)Study completedNCT00600938What this trial is testingEvaluating Use of Deferasirox as Compared to Deferoxamine in Treating Cardiac Iron OverloadWho this might be right forTransfusional Iron OverloadTransfusional Hemosiderosis Novartis Pharmaceuticals 197
Testing effectiveness (Phase 2)Study completedNCT00390858What this trial is testingA 4-year Extension Study to Core 1-year Study of Iron Chelation Therapy With Deferasirox in β-thalassemia Major Pediatric Patients With Transfusional Iron Overload.Who this might be right forTransfusional Iron Overloadβ-thalassemia MajorPediatric Rare Anemia Novartis Pharmaceuticals 40
Post-approval studies (Phase 4)Enrolling By InvitationNCT05777993What this trial is testingProvide Access to Mitapivat for Participants Who Previously Participated in an Agios-Sponsored Mitapivat StudyWho this might be right forPyruvate Kinase DeficiencyAnemia, HemolyticSickle Cell Disease+1 more Agios Pharmaceuticals, Inc. 59
Testing effectiveness (Phase 2)Active Not RecruitingNCT05567458What this trial is testingEvaluate Luspatercept (ACE-536) in Chinese Participants Who Require Regular Red Blood Cell Transfusions Due to Beta (β)-Thalassemia.Who this might be right forBeta-thalassemia Bristol-Myers Squibb 94
Early research (Phase 1)Ended earlyNCT07431398What this trial is testingSingle-dose Pharmacokinetics of Pociredir in Participants With Sickle Cell DiseaseWho this might be right forSickle Cell Disease Fulcrum Therapeutics 13
Large-scale testing (Phase 3)Study completedNCT01740531What this trial is testingStudy to Evaluate Efficacy and Safety of S303 Treated Red Blood Cells (RBCs)in Subjects With Thalassemia Major Requiring Chronic RBC TransfusionWho this might be right forThalassemia Major Cerus Corporation 86