Large-scale testing (Phase 3)Study completedNCT03070119What this trial is testingLong-Term Evaluation of BIIB067 (Tofersen)Who this might be right forALS Caused by Superoxide Dismutase 1 (SOD1) Mutation Biogen 139
Early research (Phase 1)Study completedNCT01041222What this trial is testingSafety, Tolerability, and Activity Study of ISIS SOD1Rx to Treat Familial Amyotrophic Lateral Sclerosis (ALS) Caused by SOD1 Gene MutationsWho this might be right forFamilial Amyotrophic Lateral Sclerosis Ionis Pharmaceuticals, Inc. 33