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Results for “Adeno-Associated Virus (AAV)”

82 trials

Showing 20 of 82 results

Not applicableActive Not RecruitingNCT04645212
What this trial is testing

Long-term Study of ADVM-022 in Neovascular (Wet) AMD [OPTIC-EXT]

Who this might be right for
Wet Age-related Macular DegenerationNeovascular Age-related Macular Degeneration
Adverum Biotechnologies, Inc. 23
Large-scale testing (Phase 3)Study completedNCT03569891
What this trial is testing

HOPE-B: Trial of AMT-061 in Severe or Moderately Severe Hemophilia B Patients

Who this might be right for
Hemophilia B
CSL Behring 67
Not applicableStudy completedNCT00515710
What this trial is testing

LTFU for Gene Transfer Subjects With Hemophilia B

Who this might be right for
Hemophilia B
Spark Therapeutics, Inc. 4
Early research (Phase 1)UnknownNCT01637805
What this trial is testing

Clinical Safety and Preliminary Efficacy of AAV-DC-CTL Treatment in Stage IV Gastric Cancer

Who this might be right for
Stage IV Gastric Cancer
Tianjin Medical University Cancer Institute and Hospital 30
Not applicableLooking for participantsNCT03466463
What this trial is testing

Gene Therapy for Severe Crigler Najjar Syndrome

Who this might be right for
Crigler-Najjar Syndrome
Genethon 17
Large-scale testing (Phase 3)Active Not RecruitingNCT04850118
What this trial is testing

A Clinical Trial Evaluating the Safety and Efficacy of a Single Subretinal Injection of AGTC-501 in Participants With XLRP

Who this might be right for
X-Linked Retinitis Pigmentosa
Beacon Therapeutics 85
Testing effectiveness (Phase 2)Active Not RecruitingNCT05243017
What this trial is testing

Safety and Efficacy of AMT-130 in European Adults With Early Manifest Huntington's Disease

Who this might be right for
Huntington Disease
UniQure Biopharma B.V. 14
Testing effectiveness (Phase 2)Looking for participantsNCT06641154
What this trial is testing

Gene Therapy for Crigler Najjar Syndrome Type I (AlphaCN)

Who this might be right for
Crigler-Najjar Syndrome Type I
Federal State Budget Institution Research Center for Obstetrics, Gynecology and Perinatology Ministry of Healthcare 5
Early research (Phase 1)Study completedNCT00428935
What this trial is testing

Safety Study of Mini-dystrophin Gene to Treat Duchenne Muscular Dystrophy

Who this might be right for
Duchenne Muscular Dystrophy
Nationwide Children's Hospital 6
Not applicableStudy completedNCT04135300
What this trial is testing

Gene Therapy for Chinese Hemophilia B

Who this might be right for
Hemophilia B
Institute of Hematology & Blood Diseases Hospital, China 10
Testing effectiveness (Phase 2)Study completedNCT02416622
What this trial is testing

Safety and Efficacy of rAAV-hRS1 in Patients With X-linked Retinoschisis (XLRS)

Who this might be right for
X-linked Retinoschisis
Beacon Therapeutics 27
Early research (Phase 1)Looking for participantsNCT07371338
What this trial is testing

Phase 1 Clinical Trial to Evaluate the Safety, Efficacy, and Pharmacokinetics of IPS101A in Parkinson's Disease Patients

Who this might be right for
Parkinson DiseaseParkinson's Disease
Innopeutics Corporation 6
Testing effectiveness (Phase 2)Looking for participantsNCT07443826
What this trial is testing

CALM-AF-AI: Counteracting Age-related Loss of Muscle With AAV-Follistatin Combined With Angiogenesis-Inducing VEGF Plasmid Gene Therapy

Who this might be right for
Age-related Muscle Decline
Unlimited Biotechnology LLC 12
Testing effectiveness (Phase 2)Study completedNCT01899092
What this trial is testing

Safety and Efficacy Study of Single Doses of TT-034 in Patients With Chronic Hepatitis C

Who this might be right for
Hepatitis C
Tacere Therapeutics, Inc. 9
Early research (Phase 1)Active Not RecruitingNCT05040217
What this trial is testing

A Clinical Trial of AAV2-BDNF Gene Therapy in Early Alzheimer's Disease and Mild Cognitive Impairment

Who this might be right for
Alzheimer's DiseaseMild Cognitive Impairment
Mark Tuszynski 12
Large-scale testing (Phase 3)Active Not RecruitingNCT00999609
What this trial is testing

Safety and Efficacy Study in Subjects With Leber Congenital Amaurosis

Who this might be right for
Inherited Retinal Dystrophy Due to RPE65 MutationsLeber Congenital Amaurosis
Spark Therapeutics, Inc. 31
Early research (Phase 1)Study completedNCT00494195
What this trial is testing

Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)

Who this might be right for
Muscular Dystrophies
Nationwide Children's Hospital 6
Testing effectiveness (Phase 2)Study completedNCT03588299
What this trial is testing

Study to Test the Safety and How Well Patients With Severe Hemophilia A Respond to Treatment With BAY 2599023 (DTX 201), a Drug Therapy That Delivers a Healthy Version of the Defective Factor VIII Gene Into the Nucleus of Liver Cells Using an Altered, Non-infectious Virus (AAV) as a "Shuttle"

Who this might be right for
Hemophilia A
Bayer 11
Large-scale testing (Phase 3)Active Not RecruitingNCT06856577
What this trial is testing

Efficacy and Safety Study of Ixoberogene Soroparvovec (Ixo-vec) in Participants With Neovascular Age-Related Macular Degeneration

Who this might be right for
Neovascular Age-Related Macular Degeneration (nAMD)Wet AMD
Adverum Biotechnologies, Inc. 311
Testing effectiveness (Phase 2)Looking for participantsNCT05788536
What this trial is testing

DB-OTO, an Adeno-Associated Virus (AAV) Based Gene Therapy, in Children/Infants, Adolescents and Adults With Hearing Loss Due to Otoferlin Mutations

Who this might be right for
Congenital Hearing Loss Secondary to Biallelic Mutations of the Otoferlin Gene (OTOF)
Regeneron Pharmaceuticals 36
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