Early research (Phase 1)Enrolling By InvitationNCT07412821
What this trial is testing
A Phase 1b Study of Adenylosuccinic Acid (ASA-001) for Adenylosuccinate Synthase 1 (ADSS1) Deficient Myopathy.
Who this might be right for
Adenylosuccinate Synthase 1 Deficient Myopathy
Cure ADSSL1 2