Not applicableEnded earlyNCT05020743What this trial is testingNatural History Study in Adult-Onset Leukoencephalopathy With Axonal Spheroids and Pigmented GliaWho this might be right forALSP Vigil Neuroscience, Inc. 56
Not applicableEnrolling By InvitationNCT04503213What this trial is testingAssess CSF1R-related Leukoencephalopathy After Stem Cell TransplantationWho this might be right forCSF1R-related LeukoencephalopathyALSPPOLD+1 more Mayo Clinic 20
Testing effectiveness (Phase 2)Looking for participantsNCT01962415What this trial is testingReduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCTWho this might be right forPrimary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+4 more Paul Szabolcs 100
Not applicableLooking for participantsNCT04925349What this trial is testingModeling Macrophages Activation Pattern in X-linked Adrenoleukodystrophy, Metachromatic Leukodystrophy and Adult Onset Leukoencephalopathy With Axonal Spheroids and Pigmented GliaWho this might be right forAdrenoleukodystrophyAdrenomyeloneuropathyMetachromatic Leukodystrophy+1 more Assistance Publique - Hôpitaux de Paris 100
Testing effectiveness (Phase 2)Active Not RecruitingNCT02171104What this trial is testingMT2013-31: Allo HCT for Metabolic Disorders and Severe OsteopetrosisWho this might be right forMucopolysaccharidosis DisordersHurler SyndromeHunter Syndrome+26 more Masonic Cancer Center, University of Minnesota 149
Testing effectiveness (Phase 2)Ended earlyNCT05677659What this trial is testingVGL101 in Patients With Adult-Onset Leukoencephalopathy With Axonal Spheroids and Pigmented GliaWho this might be right forALSP Vigil Neuroscience, Inc. 20