Not applicableEnded earlyNCT03034512What this trial is testingAlpers Huttenlocher Natural History StudyWho this might be right forAlpers Huttenlocher Syndrome Columbia University 2
Large-scale testing (Phase 3)Study completedNCT05218655What this trial is testingA Safety Study for Previously Treated Vatiquinone (PTC743) Participants With Inherited Mitochondrial DiseaseWho this might be right forInherited Mitochondrial Disease PTC Therapeutics 101
Large-scale testing (Phase 3)Ended earlyNCT04378075What this trial is testingEvaluate Efficacy and Safety of Vatiquinone for Treating Mitochondrial Disease in Participants With Refractory EpilepsyWho this might be right forMitochondrial DiseasesDrug Resistant EpilepsyLeigh Disease+5 more PTC Therapeutics 68
Not applicableLooking for participantsNCT01694940What this trial is testingNorth American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC)Who this might be right forMitochondrial DisordersMitochondrial Genetic DisordersMitochondrial Diseases+2 more Columbia University 1,000