Testing effectiveness (Phase 2)Active Not RecruitingNCT06816498
What this trial is testing
Personalized Antisense Oligonucleotide Therapy for A Single Participant With LMNB1 Mutation Associated Autosomal Dominant Leukodystrophy (ADLD)
Who this might be right for
Autosomal Dominant Leukodystrophy
n-Lorem Foundation 1