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Results for “B Thalassemia”

352 trials

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Showing 20 of 352 results

Not applicableUnknownNCT03894605
What this trial is testing

Dermatological Abnormalities in Beta-thalassemia Major

Who this might be right for
Beta-Thalassemia
Assiut University 125
Early research (Phase 1)Study completedNCT01752153
What this trial is testing

Immunomodulatory Effects of Silymarin in Patients With Beta-Thalassemia Major

Who this might be right for
Immune Abnormalities
Shiraz University of Medical Sciences 25
Testing effectiveness (Phase 2)UnknownNCT03183375
What this trial is testing

The Efficacy and Safety of HYDROXYUREA in Management of Beta Thalassemia Patients in Karachi Pakistan

Who this might be right for
Thalassemia, Beta
Dr.Saqib Hussain Ansari 100
Testing effectiveness (Phase 2)Study completedNCT04054921
What this trial is testing

Safety Study for Beta Thalassemia Subjects on PTG-300

Who this might be right for
β-thalassemiaIneffective Erythropoiesis
Protagonist Therapeutics, Inc. 34
Testing effectiveness (Phase 2)Study completedNCT00006136
What this trial is testing

Phase II Study of Arginine Butyrate With or Without Epoetin Alfa in Patients With Thalassemia Intermedia

Who this might be right for
Beta-Thalassemia
Boston University 15
Not applicableStudy completedNCT01931644
What this trial is testing

At-Home Research Study for Patients With Autoimmune, Inflammatory, Genetic, Hematological, Infectious, Neurological, CNS, Oncological, Respiratory, Metabolic Conditions

Who this might be right for
All Diagnosed Health ConditionsADD/ADHDAlopecia Areata+58 more
Sanguine Biosciences 17,667
Testing effectiveness (Phase 2)UnknownNCT00061568
What this trial is testing

Improving the Results of Bone Marrow Transplantation for Patients With Severe Congenital Anemias

Who this might be right for
Congenital Hemolytic AnemiaSickle Cell Disease
National Heart, Lung, and Blood Institute (NHLBI) 130
Not applicableUnknownNCT03951818
What this trial is testing

Observing the Changes of Endocrine and Metabolism in Patients With Thalassemia Major

Who this might be right for
Thalassemia Major
National Taiwan University Hospital 100
Large-scale testing (Phase 3)Looking for participantsNCT04064060
What this trial is testing

Evaluate Long-term Safety in Participants Who Have Participated in Other Luspatercept (ACE-536) Clinical Trials

Who this might be right for
Myelodysplastic Syndromes (MDS)Beta-thalassemiaMyeloproliferative Neoplasm(MPN)-Associated Myelofibrosis
Celgene 665
Large-scale testing (Phase 3)Study completedNCT03655678
What this trial is testing

A Safety and Efficacy Study Evaluating CTX001 in Participants With Transfusion-Dependent β-Thalassemia

Who this might be right for
Beta-ThalassemiaThalassemiaGenetic Diseases, Inborn+2 more
Vertex Pharmaceuticals Incorporated 59
Post-approval studies (Phase 4)UnknownNCT05462548
What this trial is testing

The Safety and Efficiency of Luspatercept in Chinese Adults With Transfusion Dependent β-thalassemia: a Real-world Study

Who this might be right for
Thalassemia MajorTransfusion-dependent Anemia
Sun Yat-sen University 20
Not applicableNot Yet RecruitingNCT04219449
What this trial is testing

Thrombophilia In Beta Thalassemia

Who this might be right for
Beta-Thalassemia
Assiut University 100
Not applicableUnknownNCT01201135
What this trial is testing

GDF 15 in Sickle Cell Disease and Hereditary Spherocytosis

Who this might be right for
Patients With Thalassemia Intermedia,Congenital Dyserythropoietic Anemia Type I
Wolfson Medical Center 80
Not applicableStudy completedNCT02308904
What this trial is testing

Reproductive Capacity and Iron Burden in Thalassemia

Who this might be right for
THALASSEMIA MAJOR
UCSF Benioff Children's Hospital Oakland 59
Not applicableUnknownNCT02428023
What this trial is testing

B-Thalasaemia Trait and Its Possible Cardioprotective Role

Who this might be right for
Beta-Thalassemia TraitCoronary Artery Disease
404 General Military Hospital, Larissa 2,500
Not applicableUnknownNCT05105659
What this trial is testing

Assessment of Cognitive Functions, Psychological Symptoms, and Quality of Life Among B Thalassemia Patients and Their Clinical Correlates.

Who this might be right for
B Thalassemia
Assiut University 60
Testing effectiveness (Phase 2)Study completedNCT01740713
What this trial is testing

Pharmacokinetic Study of Deferiprone in Paediatric Patients

Who this might be right for
Chronic Iron Overload
Consorzio per Valutazioni Biologiche e Farmacologiche 23
Not applicableActive Not RecruitingNCT06875219
What this trial is testing

To Evaluate Long- Term Safety and Efficacy of Luspatercept

Who this might be right for
Thalassemia Major
Fondazione per la Ricerca sulle Anemie ed Emoglobinopatie in Italia 350
Large-scale testing (Phase 3)Study completedNCT01863173
What this trial is testing

Effect of Metoprolol on Thalassemia Cardiomyopathy

Who this might be right for
B Thalassemia
Shiraz University of Medical Sciences 45
Testing effectiveness (Phase 2)UnknownNCT03276455
What this trial is testing

Gene Therapy for Beta-Thalassemia Major Using Autologous Hematopoietic Stem Cell Genetically Modified

Who this might be right for
Beta Thalassemia Major
Nanfang Hospital, Southern Medical University 10
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