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Results for “B Thalassemia Major”

168 trials

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Showing 20 of 168 results

Testing effectiveness (Phase 2)Study completedNCT00005934
What this trial is testing

5-Azacytidine and Phenylbutyrate to Treat Severe Thalassemia

Who this might be right for
Beta Thalassemia
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) 24
Very early researchLooking for participantsNCT05745532
What this trial is testing

Safety and Efficacy Evaluation of β-globin Restored Autologous Hematopoietic Stem Cells in β-thalassemia Major Patients

Who this might be right for
β-thalassemia
Shenzhen Hemogen 10
Early research (Phase 1)Ended earlyNCT02986698
What this trial is testing

In Utero Hematopoietic Stem Cell Transplantation for Alpha-thalassemia Major (ATM)

Who this might be right for
Alpha Thalassemia MajorHemoglobinopathy; With ThalassemiaHemoglobinopathies+6 more
University of California, San Francisco 6
Not applicableStudy completedNCT07486531
What this trial is testing

Iron Accumulation in Erythrocytes in Patients

Who this might be right for
Beta Thalassemia Major
Ankara City Hospital Bilkent 100
Not applicableStudy completedNCT03170245
What this trial is testing

Adiponectin, IL-6 and hsC-RP in Relation to Carotid Intima-media Thickness in B-thalassemia Patients

Who this might be right for
Thalassemia
Assiut University 85
Not applicableEnrolling By InvitationNCT03655223
What this trial is testing

Early Check: Expanded Screening in Newborns

Who this might be right for
Spinal Muscular AtrophyFragile X SyndromeFragile X - Premutation+182 more
RTI International 30,000
Not applicableUnknownNCT06137079
What this trial is testing

"Iron Overload and Endocrinological Diseases"

Who this might be right for
Iron OverloadThalassemia MajorThalassemia Intermedia+2 more
Azienda Ospedaliero-Universitaria di Modena 62
Not applicableLooking for participantsNCT06734520
What this trial is testing

Clinical Study of Super Transplantation in the Treatment of Severe β-thalassemia

Who this might be right for
Thalassemia Majors (Beta-Thalassemia Major)Haplo-identical Donors
Guangzhou Women and Children's Medical Center 3
Testing effectiveness (Phase 2)Looking for participantsNCT03653338
What this trial is testing

T-Cell Depleted Alternative Donor Bone Marrow Transplant for Sickle Cell Disease (SCD) and Other Anemias

Who this might be right for
Sickle Cell AnemiaBeta-thalassemia MajorDiamond-blackfan Anemia
Paul Szabolcs 5
Not applicableStudy completedNCT04526405
What this trial is testing

Frequency of COVID-19 Antibodies in Patients With Hereditary Hematological Diseases

Who this might be right for
Thalassemia MajorCovid19
University of Milano Bicocca 63
Not applicableTemporarily pausedNCT05442346
What this trial is testing

Safety and Efficacy Evaluation of γ-globin Reactivated Autologous Hematopoietic Stem Cells

Who this might be right for
Thalassemia Major
Bioray Laboratories 5
Testing effectiveness (Phase 2)Study completedNCT02049450
What this trial is testing

Study of Efficacy and Safety of INC424 in Regularly Transfused Patients With Thalassemia.

Who this might be right for
Thalassemia Major
Novartis Pharmaceuticals 30
Not applicableStudy completedNCT04211480
What this trial is testing

Safety and Efficacy Evaluation of γ-globin Reactivated Autologous Hematopoietic Stem Cells

Who this might be right for
β Thalassemia Major
Bioray Laboratories 6
Not applicableStudy completedNCT01206075
What this trial is testing

Evaluating the Safety and Effectiveness of Mozobil Mobilization in Adults With Beta-Thalassemia Major

Who this might be right for
Beta-Thalassemia
University of Washington 20
Post-approval studies (Phase 4)Study completedNCT03095326
What this trial is testing

Pneumococcal Vaccination for Splenectomised Thalassemia Major Patients in Indonesia

Who this might be right for
ThalassemiaPneumococcal Infection
Fakultas Kedokteran Universitas Indonesia 56
Not applicableStudy completedNCT02308904
What this trial is testing

Reproductive Capacity and Iron Burden in Thalassemia

Who this might be right for
THALASSEMIA MAJOR
UCSF Benioff Children's Hospital Oakland 59
Not applicableStudy completedNCT02744105
What this trial is testing

Effect of Spirulina on Liver Fibrosis by Transient Elastography in Beta Thalassemic Children With Hepatitis C

Who this might be right for
Beta Thalassemia Major
Tanta University 60
Large-scale testing (Phase 3)Study completedNCT00171171
What this trial is testing

Long-term Treatment With Deferasirox in Patients With Beta-thalassemia and Transfusional Hemosiderosis

Who this might be right for
Beta-ThalassemiaHemosiderosis
Novartis 252
Large-scale testing (Phase 3)UnknownNCT01511848
What this trial is testing

Study Of Efficacy,Safety of Combined Deferasirox and Deferiprone Versus Combined Deferiprone and Desferal In Conditions of Iron Overload

Who this might be right for
Beta-thalassemia MajorSickle Cell DiseaseIron Hemosiderosis
Ain Shams University 60
Not applicableStudy completedNCT00004378
What this trial is testing

Stem Cell Transplantation (SCT) for Genetic Diseases

Who this might be right for
ThrombocytopeniaMetachromatic LeukodystrophyFanconi's Anemia+3 more
National Center for Research Resources (NCRR)
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