Crick
HomeTrialsGenesDrugs23andMeGraphBlogContact
  • Home
  • Trials
  • Genes
  • Drugs
  • 23andMe
  • Graph
  • Blog
  • Contact
Crick

An open-source clinical intelligence platform. Explore clinical trials, gene networks, and molecular structures using public data sources.

Data Sources

  • ClinicalTrials.gov
  • OpenTargets
  • ClinVar
  • PubChem

Links

  • Contact
  • Privacy

© 2026 Crick. All rights reserved.

Crick is for educational purposes only. Not medical advice.

Results for “Batten Disease”

Filters

Phase
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Status
Recruiting
Active, Not Recruiting
Not Yet Recruiting
Completed
Enrolling by Invitation

Showing 11 of 0 results

Not applicableEnrolling By InvitationNCT03862274
What this trial is testing

Examining Developmental Outcomes of Children Diagnosed With CLN2 Disease

Who this might be right for
Batten DiseaseCLN2Neuronal Ceroid-Lipofuscinoses
Jessica Scherr 30
Large-scale testing (Phase 3)Study completedNCT00176904
What this trial is testing

Stem Cell Transplant for Inborn Errors of Metabolism

Who this might be right for
AdrenoleukodystrophyMetachromatic LeukodystrophyGloboid Cell Leukodystrophy+8 more
Masonic Cancer Center, University of Minnesota 135
Testing effectiveness (Phase 2)Not Yet RecruitingNCT07582484
What this trial is testing

Gene Therapy Trial for CLN6 Batten Disease

Who this might be right for
CLN6Batten DiseaseBatten's Disease+2 more
The Charlotte and Gwenyth Gray Foundation 12
Not applicableActive Not RecruitingNCT04273243
What this trial is testing

Long-Term Follow Up of CLN6 Batten Disease Subjects Following Gene Transfer

Who this might be right for
CLN6Batten Disease
Emily de los Reyes 10
Testing effectiveness (Phase 2)Not Yet RecruitingNCT07740512
What this trial is testing

Safety, Tolerability, Pharmacokinetics, and Preliminary Efficacy of PLX-200 in Pediatric Patients (Master Protocol)

Who this might be right for
Lysosomal Storage DisordersSandhoff DiseaseKrabbe Disease+2 more
Polaryx Therapeutics, Inc. 24
Large-scale testing (Phase 3)WithdrawnNCT04637282
What this trial is testing

Safety, Tolerability, and Efficacy of PLX-200 in Patients With CLN3

Who this might be right for
Juvenile Neuronal Ceroid Lipofuscinosis
Polaryx Therapeutics, Inc.
Post-approval studies (Phase 4)Study completedNCT00028262
What this trial is testing

Cystagon to Treat Infantile Neuronal Ceroid Lipofuscinosis

Who this might be right for
Infantile Neronal Ceroid Lipofuscinosis
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) 10
Not applicableLooking for participantsNCT06203106
What this trial is testing

NYSCF Scientific Discovery Biobank

Who this might be right for
ALSAmyotrophic Lateral SclerosisAlzheimer Disease+26 more
New York Stem Cell Foundation Research Institute 10,000
Not applicableWithdrawnNCT04480476
What this trial is testing

A Retrospective, Natural History Study in Children With CLN2

Who this might be right for
Late-infantile Neuronal Ceroid Lipofuscinosis Type 2 (CLN2)
REGENXBIO Inc.
Not applicableLooking for participantsNCT01793168
What this trial is testing

Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford

Who this might be right for
Rare DisordersUndiagnosed DisordersDisorders of Unknown Prevalence+340 more
Sanford Health 20,000
Early research (Phase 1)Looking for participantsNCT02254863
What this trial is testing

UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells

Who this might be right for
AdrenoleukodystrophyBatten DiseaseMucopolysaccharidosis II+9 more
Joanne Kurtzberg, MD 40