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Results for “Biallelic RPE65 Mutation-associated Retinal Dystrophy”

6 trials

Showing 6 of 6 results

Large-scale testing (Phase 3)Active Not RecruitingNCT07054632
What this trial is testing

Efficacy and Safety of LX101 for Inherited Retinal Dystrophy Associated With RPE65 Mutations

Who this might be right for
Inherited Retinal Dystrophy Associated With RPE65 Mutations
Innostellar Biotherapeutics Co.,Ltd 30
Testing effectiveness (Phase 2)Active Not RecruitingNCT06212297
What this trial is testing

Fellow-eye Study (FE) of LX101 in Subjects With Inherited Retinal Dystrophy

Who this might be right for
Inherited Retinal Dystrophy
Innostellar Biotherapeutics Co.,Ltd 9
Large-scale testing (Phase 3)Active Not RecruitingNCT04516369
What this trial is testing

Study of Efficacy and Safety of Voretigene Neparvovec in Japanese Patients With Biallelic RPE65 Mutation-associated Retinal Dystrophy

Who this might be right for
Biallelic RPE65 Mutation-associated Retinal Dystrophy
Novartis Pharmaceuticals 4
Testing effectiveness (Phase 2)Looking for participantsNCT05858983
What this trial is testing

Gene Therapy in Subjects With Biallelic RPE65 Mutation-associated Retinal Dystrophy

Who this might be right for
Biallelic RPE65 Mutation-associated Retinal Dystrophy
Frontera Therapeutics 9
Not applicableStudy completedNCT03597399
What this trial is testing

A Patient Registry Study for Patients Treated With Voretigene Neparvovec in US

Who this might be right for
Confirmed Biallelic RPE65 Mutation-associated Retinal Dystrophy
Spark Therapeutics, Inc. 87
Testing effectiveness (Phase 2)Active Not RecruitingNCT06196827
What this trial is testing

Safety and Tolerability of LX101 for Inherited Retinal Dystrophy Associated With RPE65 Mutations

Who this might be right for
Inherited Retinal Dystrophy Associated With RPE65 Mutations
Innostellar Biotherapeutics Co.,Ltd 9

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