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Results for “CAH - Congenital Adrenal Hyperplasia”

39 trials

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Showing 20 of 39 results

Not applicableLooking for participantsNCT00250159
What this trial is testing

Natural History Study of Patients With Excess Androgen

Who this might be right for
Congenital Adrenal Hyperplasia (CAH)Familial Male-Limited Precocious Puberty (FMPP)
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) 3,000
Testing effectiveness (Phase 2)Ended earlyNCT04457336
What this trial is testing

A Ph2b to Evaluate Clinical Efficacy and Safety of Tildacerfont in Adult CAH

Who this might be right for
Congenital Adrenal Hyperplasia
Spruce Biosciences 96
Testing effectiveness (Phase 2)Study completedNCT00519818
What this trial is testing

Comparison of Two Forms of Hydrocortisone in Patients With Congenital Adrenal Hyperplasia

Who this might be right for
Congenital Adrenal Hyperplasia21-Hydroxylase DeficiencyAdrenogenital Syndrome
Neurocrine UK Limited 20
Testing effectiveness (Phase 2)Not Yet RecruitingNCT07536269
What this trial is testing

Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Crinecerfont in Participants With Classic Congenital Adrenal Hyperplasia (CAH) Who Are Less Than 4 Years Old

Who this might be right for
Congenital Adrenal Hyperplasia
Neurocrine Biosciences 20
Not applicableStudy completedNCT05101902
What this trial is testing

Determine Eligibility for CAH-301 (A Study of Gene Therapy for Classic Congenital Adrenal Hyperplasia (CAH) [NCT04783181])

Who this might be right for
Congenital Adrenal Hyperplasia
Adrenas Therapeutics Inc 65
Not applicableStudy completedNCT00559078
What this trial is testing

Qualitative Research on Women With Congenital Adrenal Hyperplasia

Who this might be right for
Congenital Adrenal Hyperplasia
Lehigh University 16
Testing effectiveness (Phase 2)Study completedNCT01735617
What this trial is testing

Pilot Study to Characterize and Examine the Pharmacokinetics and Efficacy of Chronocort® in Adults With CAH

Who this might be right for
Endocrine DiseaseAdrenal InsufficiencyCongenital Adrenal Hyperplasia
Neurocrine UK Limited 16
Testing effectiveness (Phase 2)Active Not RecruitingNCT04783181
What this trial is testing

Gene Therapy for Classic Congenital Adrenal Hyperplasia (CAH)

Who this might be right for
Congenital Adrenal Hyperplasia
Adrenas Therapeutics Inc 8
Testing effectiveness (Phase 2)Study completedNCT01859312
What this trial is testing

Comparison of Cortisol Pump With Standard Treatment for Congenital Adrenal Hyperplasia

Who this might be right for
Adrenal InsufficiencyExcess AndrogenCongenital Adrenal Hyperplasia (CAH)
National Institutes of Health Clinical Center (CC) 8
Not applicableStudy completedNCT06449456
What this trial is testing

Exercise Capacity, Physical Fitness, and Physical Activity Levels in Children With CAH

Who this might be right for
Congenital Adrenal HyperplasiaExercise CapacityPhysical Activity+1 more
Hacettepe University 48
Large-scale testing (Phase 3)Active Not RecruitingNCT04806451
What this trial is testing

Global Safety and Efficacy Registration Study of Crinecerfont in Pediatric Participants With Classic Congenital Adrenal Hyperplasia (CAHtalyst Pediatric Study)

Who this might be right for
Congenital Adrenal Hyperplasia
Neurocrine Biosciences 103
Not applicableEnded earlyNCT01661387
What this trial is testing

A European Post-Authorisation Observational Study (Registry) of Patients With Chronic Adrenal Insufficiency (AI)

Who this might be right for
Chronic Adrenal Insufficiency
Shire 3,258
Testing effectiveness (Phase 2)Ended earlyNCT04544410
What this trial is testing

A Ph2b to Evaluate Tildacerfont in the Reduction of Glucocorticoid Steroid Doses in Adult CAH

Who this might be right for
Congenital Adrenal Hyperplasia
Spruce Biosciences 100
Not applicableNot Yet RecruitingNCT07622030
What this trial is testing

Hydrocortisone Modified-release in Adults: Real-world Monitoring of Longitudinal Outcomes in coNgenital Adrenal hYperplasia

Who this might be right for
CAH - Congenital Adrenal Hyperplasia
IRCCS San Raffaele 100
Testing effectiveness (Phase 2)Study completedNCT03525886
What this trial is testing

Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of NBI-74788 in Adults With Congenital Adrenal Hyperplasia

Who this might be right for
CAH - Congenital Adrenal Hyperplasia
Neurocrine Biosciences 18
Testing effectiveness (Phase 2)Ended earlyNCT05128942
What this trial is testing

Evaluate the Safety, Efficacy and PK of Tildacerfont in Children Aged 2-17 Years With CAH

Who this might be right for
Congenital Adrenal Hyperplasia21-OHD
Spruce Biosciences 67
Not applicableUnknownNCT05162950
What this trial is testing

Effects and Importance of Epinephrine/Adrenalin Deficiency in CAH

Who this might be right for
Congenital Adrenal Hyperplasia
Region Stockholm 120
Not applicableStudy completedNCT00011791
What this trial is testing

Catecholamine Reserve and Exercise Tolerance in Healthy Volunteers and Patients With Congenital Adrenal Hyperplasia

Who this might be right for
Congenital Adrenal HyperplasiaHealthy
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) 61
Testing effectiveness (Phase 2)Looking for participantsNCT06712823
What this trial is testing

An Extension Study to Evaluate Safety and Efficacy in Participants Treated With CRN04894

Who this might be right for
Congenital Adrenal HyperplasiaClassic Congenital Adrenal Hyperplasia
Crinetics Pharmaceuticals Inc. 150
Testing effectiveness (Phase 2)Looking for participantsNCT07187375
What this trial is testing

Pharmacokinetics, Safety and Tolerability of Crinecerfont in Participants With Congenital Adrenal Hyperplasia Who Are Less Than 2 Years Old

Who this might be right for
Congenital Adrenal Hyperplasia
Neurocrine Biosciences 6
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