Testing effectiveness (Phase 2)UnknownNCT03404869What this trial is testingStudy of ORL-1M (D-mannose) in Patients With CDG-IbWho this might be right forCDG Ib Orpha Labs 5
Not applicableEnrolling By InvitationNCT03655223What this trial is testingEarly Check: Expanded Screening in NewbornsWho this might be right forSpinal Muscular AtrophyFragile X SyndromeFragile X - Premutation+182 more RTI International 30,000