Testing effectiveness (Phase 2)Enrolling By InvitationNCT05152823What this trial is testingGene Therapy for IGHMBP2-Related DiseasesWho this might be right forSMARD1CMT2S Megan Waldrop 10
Testing effectiveness (Phase 2)Active Not RecruitingNCT07223632What this trial is testingTreatment of Charcot-Marie-Tooth Disease, Axonal, Type 2S (CMT2S) in an Individual PatientWho this might be right forCharcot Marie Tooth Disease (CMT)Neuromuscular Diseases (NMD) Vanda Pharmaceuticals 1