Not applicableEnded earlyNCT05020743What this trial is testingNatural History Study in Adult-Onset Leukoencephalopathy With Axonal Spheroids and Pigmented GliaWho this might be right forALSP Vigil Neuroscience, Inc. 56
Not applicableLooking for participantsNCT03047369What this trial is testingThe Myelin Disorders Biorepository ProjectWho this might be right forLeukodystrophyWhite Matter DiseaseLeukoencephalopathies+63 more Children's Hospital of Philadelphia 12,000
Not applicableStudy completedNCT02699190What this trial is testingLeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for LeukodystrophiesWho this might be right forLeukodystrophyWhite Matter Disease4H Syndrome+61 more Children's Hospital of Philadelphia 236
Testing effectiveness (Phase 2)Active Not RecruitingNCT02171104What this trial is testingMT2013-31: Allo HCT for Metabolic Disorders and Severe OsteopetrosisWho this might be right forMucopolysaccharidosis DisordersHurler SyndromeHunter Syndrome+26 more Masonic Cancer Center, University of Minnesota 149
Testing effectiveness (Phase 2)Ended earlyNCT05677659What this trial is testingVGL101 in Patients With Adult-Onset Leukoencephalopathy With Axonal Spheroids and Pigmented GliaWho this might be right forALSP Vigil Neuroscience, Inc. 20
Early research (Phase 1)Active Not RecruitingNCT03993873What this trial is testingStudy of TPX-0022 in Patients With Advanced NSCLC, Gastric Cancer or Solid Tumors Harboring Genetic Alterations in METWho this might be right forAdvanced Solid TumorMetastatic Solid TumorsMET Gene Alterations Turning Point Therapeutics, Inc. 95