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Results for “Carnitine Palmitoyltransferase Deficiencies (CPT1, CPT2)”

3 trials

Showing 3 of 3 results

Not applicableEnded earlyNCT04812106
What this trial is testing

Long-Chain Fatty Acid Oxidation Disorders Online Disease Monitoring Program

Who this might be right for
Long-chain Fatty Acid Oxidation Disorders (LC-FAOD)
Ultragenyx Pharmaceutical Inc 8
Not applicableNo Longer AvailableNCT01461304
What this trial is testing

Compassionate Use of Triheptanoin (C7) for Inherited Disorders of Energy Metabolism

Who this might be right for
Very Long-chain acylCoA Dehydrogenase (VLCAD) DeficiencyCarnitine Palmitoyltransferase Deficiencies (CPT1, CPT2)Mitochondrial Trifunctional Protein Deficiency+5 more
Jerry Vockley, MD, PhD
Not applicableActive Not RecruitingNCT04632953
What this trial is testing

Long-Chain Fatty Acid Oxidation Disorders In-Clinic Disease Monitoring Program

Who this might be right for
Long-chain Fatty Acid Oxidation Disorders (LC-FAOD)
Ultragenyx Pharmaceutical Inc 150

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