Large-scale testing (Phase 3)Active Not RecruitingNCT06247085
What this trial is testing
Investigate Efficacy and Safety of Pegtibatinase Compared With Placebo in Participants ≥12 to ≤65 Years of Age With Classical Homocystinuria (HCU) Due to Cystathionine Beta Synthase Deficiency Receiving Standard of Care Treatment
Who this might be right for
Homocystinuria
Travere Therapeutics, Inc. 70