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Results for “Classical Phenylketonuria(PKU)”

158 trials

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Showing 20 of 158 results

Not applicableWithdrawnNCT01650909
What this trial is testing

The Effects of Sapropterin Dihydrochloride Supplementation on in Vivo Redox Status in Patients With Classical PKU

Who this might be right for
Classical Phenylketonuria(PKU)
Stanford University
Testing effectiveness (Phase 2)Study completedNCT03516487
What this trial is testing

Safety and Tolerability of SYNB1618 in Healthy Adult Volunteers and Adult Subjects With Phenylketonuria

Who this might be right for
PhenylketonuriaHealthy
Synlogic 70
Early research (Phase 1)Ended earlyNCT05222178
What this trial is testing

Safety and Efficacy of HMI-103 in Participants With Classical PKU Due to PAH Deficiency

Who this might be right for
PhenylketonuriasPAH DeficiencyPhenylketonuria
Homology Medicines, Inc 3
Not applicableEnded earlyNCT01904708
What this trial is testing

Moderate Intensity Exercise and Phenylketonuria

Who this might be right for
PhenylketonuriaPKU
Oregon Health and Science University 2
Large-scale testing (Phase 3)Study completedNCT01376908
What this trial is testing

Kuvan® in Phenylketonuria Patients Less Than 4 Years Old

Who this might be right for
Phenylketonuria
BioMarin Pharmaceutical 56
Testing effectiveness (Phase 2)Study completedNCT01560286
What this trial is testing

Evaluate Subcutaneously Administered rAvPAL-PEG in Patients With Phenylketonuria for 24 Weeks

Who this might be right for
Phenylketonuria
BioMarin Pharmaceutical 24
Early research (Phase 1)Ended earlyNCT04110496
What this trial is testing

Safety and Tolerability of RTX-134 in Adults With Phenylketonuria

Who this might be right for
Phenylketonurias
Rubius Therapeutics 1
Not applicableStudy completedNCT04375592
What this trial is testing

Acceptability and Tolerance of a Ready-to-use Protein Substitute in Tablet Form for the Dietary Management of Phenylketonuria

Who this might be right for
PhenylketonuriasHyperphenylalaninaemiaTetrahydrobiopterin Deficiency
metaX Institut fuer Diatetik GmbH 10
Not applicableStudy completedNCT00778206
What this trial is testing

PKUDOS: Phenylketonuria (PKU) Demographic, Outcomes, and Safety Registry

Who this might be right for
PhenylketonuriaHyperphenylalaninaemia
BioMarin Pharmaceutical 1,887
Large-scale testing (Phase 3)Study completedNCT00104247
What this trial is testing

Study to Evaluate the Safety and Efficacy of Phenoptin™ in Subjects With Phenylketonuria Who Have Elevated Phenylalanine Levels

Who this might be right for
Phenylketonurias
BioMarin Pharmaceutical 89
Not applicableStudy completedNCT05497050
What this trial is testing

The Effect of Nursing Empowerment Program

Who this might be right for
Phenylketonurias
Cukurova University 36
Early research (Phase 1)Study completedNCT00634660
What this trial is testing

Safety and Tolerability Study of rAvPAL-PEG to Treat Phenylketonuria

Who this might be right for
Phenylketonuria
BioMarin Pharmaceutical 25
Testing effectiveness (Phase 2)Study completedNCT00841100
What this trial is testing

Kuvan Therapy in Phenylketonuria (PKU): The Effect of Blood Phenylalanine Concentration on Kuvan Response

Who this might be right for
Phenylketonuria
University of Miami 21
Not applicableWithdrawnNCT04272736
What this trial is testing

PKU Low Calorie Drink Study

Who this might be right for
PhenylketonuriasHyperphenylalaninaemia
Nutricia UK Ltd
Not applicableStudy completedNCT01869972
What this trial is testing

Biological Variation of Phenylalanine in Patients With Hyperphenylalaninemia

Who this might be right for
PhenylketonuriaHyperphenylalaninemia
Hamilton Health Sciences Corporation 32
Post-approval studies (Phase 4)Study completedNCT02677870
What this trial is testing

The Effectiveness of Kuvan in Amish PKU Patients

Who this might be right for
Phenylketonuria
University Hospitals Cleveland Medical Center 7
Early research (Phase 1)Study completedNCT04085666
What this trial is testing

Pharmacodynamics, Safety, Tolerability and Pharmacokinetics of CDX-6114 in Patients With Phenylketonuria (PKU)

Who this might be right for
Phenylketonuria
Société des Produits Nestlé (SPN) 18
Testing effectiveness (Phase 2)Study completedNCT00104260
What this trial is testing

Study to Evaluate the Response to and Safety of an 8-Day Course of Phenoptin™ Treatment in Subjects With Phenylketonuria

Who this might be right for
Phenylketonurias
BioMarin Pharmaceutical 700
Testing effectiveness (Phase 2)Active Not RecruitingNCT05781399
What this trial is testing

First-in-Human, Multiple Part Clinical Study of JNT-517 in Healthy Participants and in Participants With Phenylketonuria

Who this might be right for
Phenylketonuria
Otsuka Pharmaceutical Development & Commercialization, Inc. 135
Not applicableStudy completedNCT03792451
What this trial is testing

Nutrition Status of Adults Treated With Pegvaliase

Who this might be right for
Phenylketonurias
Boston Children's Hospital 18
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