Early research (Phase 1)Active Not RecruitingNCT01639690
What this trial is testing
SS-Thalassemia Major With Autologous CD34+ Hematopoietic Progenitor Cells Transduced With TNS9.3.55 a Lentiviral Vector Encoding the Normal Human ß-Globin Gene
Who this might be right for
Confirmed Diagnosis of ß-thalassemia Major
San Rocco Therapeutics 10