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Results for “Congenital Anemias”

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Showing 20 of 0 results

Not applicableStudy completedNCT02410811
What this trial is testing

Novel Cardiac Magnetic Resonance Imaging to Define a Unique Restrictive Cardiomyopathy in Sickle Cell Disease

Who this might be right for
Sickle Cell Disease
Children's Hospital Medical Center, Cincinnati 33
Large-scale testing (Phase 3)Study completedNCT01031992
What this trial is testing

Tranexamic Acid and Epistaxis in Hereditary Hemorrhagic Telangiectasia (HHT)

Who this might be right for
Hereditary Hemorrhagic Telangiectasia
University Hospital, Saarland 23
Early research (Phase 1)Looking for participantsNCT07476183
What this trial is testing

Assessing the Safety, Tolerability, and Efficacy of APR-2020 in Pediatric and Adolescent Subjects With RPS19 Deficient Diamond-Blackfan Anemia

Who this might be right for
RPS19 Deficient Diamond-Blackfan Anemia
Apriligen, Inc. 4
Not applicableAvailableNCT01995305
What this trial is testing

Use Massive Parallel Sequencing and Exome Capture Technology to Sequence the Exome of Fanconi Anemia Children and Their Patents

Who this might be right for
Fanconi AnemiaAutosomal or Sex Linked Recessive Genetic DiseaseBone Marrow Hematopoiesis Failure, Multiple Congenital Abnormalities, and Susceptibility to Neoplastic Diseases.+1 more
Xiaofan Zhu
Testing effectiveness (Phase 2)Looking for participantsNCT06839456
What this trial is testing

Phase 1/2: CD45RA Depleted Stem Cell Addback to Prevent Viral or Fungal Infections Post TCRab/CD19 Depleted HSCT

Who this might be right for
LeukemiaHigh Risk Acute Lymphoblastic LeukemiaHigh Risk Acute Myeloid Leukemia+11 more
Children's Hospital of Philadelphia 100
Testing effectiveness (Phase 2)Ended earlyNCT02336373
What this trial is testing

Treatment of Hemoglobin SC Disease With Hydroxyurea

Who this might be right for
Hemoglobin SC Disease
Baylor College of Medicine 32
Not applicableLooking for participantsNCT06477289
What this trial is testing

Peripheral Arterial Tonometry and Neurocognition in Sickle Cell Disease

Who this might be right for
Sickle Cell Disease
St. Jude Children's Research Hospital 65
Testing effectiveness (Phase 2)Not Yet RecruitingNCT05469828
What this trial is testing

Crizanlizumab Improves Tissue Oxygen Supply Demand Matching in Patients With Sickle Cell Anemia

Who this might be right for
Sickle Cell Disease
Children's Hospital Los Angeles 30
Testing effectiveness (Phase 2)Study completedNCT00301834
What this trial is testing

Alemtuzumab, Fludarabine, and Busulfan Followed By Donor Stem Cell Transplant in Treating Young Patients With Hematologic Disorders

Who this might be right for
Congenital Amegakaryocytic ThrombocytopeniaDiamond-blackfan AnemiaLeukemia+2 more
University of California, San Francisco 35
Early research (Phase 1)Study completedNCT00243399
What this trial is testing

Oxandrolone for the Treatment of Bone Marrow Aplasia in Fanconi Anemia

Who this might be right for
Fanconi Anemia
Children's Hospital Medical Center, Cincinnati 10
Large-scale testing (Phase 3)Study completedNCT00000592
What this trial is testing

Stroke Prevention in Sickle Cell Anemia (STOP 1)

Who this might be right for
Anemia, Sickle CellCerebral Embolism and ThrombosisCerebrovascular Disorders+2 more
Augusta University
Not applicableActive Not RecruitingNCT03376893
What this trial is testing

Epidemiology of Silent and Overt Strokes in Sickle Cell Disease

Who this might be right for
Anemia, Sickle CellSickle Cell DiseaseStroke+2 more
Vanderbilt University Medical Center 102
Not applicableStudy completedNCT05387564
What this trial is testing

Increasing Documentation and Disclosure of Sickle Cell Trait Status: An Implementation Science Approach

Who this might be right for
Sickle Cell Trait
Nemours Children's Clinic 114
Not applicableStudy completedNCT04930328
What this trial is testing

Retrospective Real World Oxbryta® Data Collection and Analysis Study

Who this might be right for
Sickle Cell Disease
Pfizer 216
Early research (Phase 1)Study completedNCT04536792
What this trial is testing

Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AG-946 in Healthy Volunteers and in Participants With Sickle Cell Disease

Who this might be right for
Healthy VolunteersAnemia, Sickle Cell
Agios Pharmaceuticals, Inc. 122
Not applicableStudy completedNCT03488264
What this trial is testing

Stigma, Self-management, & Quality of Life in SCD

Who this might be right for
Sickle Cell DiseaseQuality of LifeStigma, Social+1 more
Duke University 102
Very early researchEnded earlyNCT00257543
What this trial is testing

SALT: Alternative Donor Bone Marrow and Cord Blood Transplantation for High Risk Sickle Cell Disease

Who this might be right for
Sickle Cell Disease
Emory University 3
Early research (Phase 1)Study completedNCT00270478
What this trial is testing

Hydroxyurea and Erythropoietin to Treat Sickle Cell Anemia

Who this might be right for
Sickle Cell DiseaseChronic Kidney DiseasePulmonary Hypertension
National Heart, Lung, and Blood Institute (NHLBI) 7
Testing effectiveness (Phase 2)Study completedNCT03401112
What this trial is testing

IMR-687 in Adult Participants With Sickle Cell Anemia (Homozygous HbSS or Sickle-β0 Thalassemia)

Who this might be right for
Sickle Cell Disease
Cardurion Pharmaceuticals, Inc. 100
Not applicableLooking for participantsNCT06271512
What this trial is testing

Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel

Who this might be right for
Beta-Thalassemia
Genetix Biotherapeutics Inc. 150
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