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Results for “Congenital Anemias”

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Showing 20 of 0 results

Not applicableStudy completedNCT00658385
What this trial is testing

Assess the Feasibility and Safety of Granulocyte Colony Stimulating Factor (GCSF) Mobilization of CD34+ Hematopoietic Progenitor Cells in Patients With Betathalassemia Major

Who this might be right for
Beta Thalassemia MajorCongenital Anemias
Memorial Sloan Kettering Cancer Center 5
Not applicableUnknownNCT03027258
What this trial is testing

Point-of-Delivery Prenatal Test Results Through mHealth to Improve Birth Outcome

Who this might be right for
HIVSickle Cell DiseaseHepatitis B
University of Nevada, Las Vegas 300
Not applicableStudy completedNCT01639950
What this trial is testing

Validating Pain Scales in Children and Young Adults

Who this might be right for
Sickle Cell DiseaseSolid TumorLeukemia+1 more
National Cancer Institute (NCI) 252
Not applicableStudy completedNCT01758250
What this trial is testing

Microvascular and Fibrosis Imaging Study

Who this might be right for
Autoimmune DiseasesSickle Cell DiseaseChronic Graft Versus Host Disease
Duke University 63
Not applicableStudy completedNCT04057521
What this trial is testing

Coordinated HEalthcare for Complex Kids

Who this might be right for
AsthmaDiabetes MellitusSickle Cell Disease+1 more
University of Illinois at Chicago 6,259
Testing effectiveness (Phase 2)WithdrawnNCT00538564
What this trial is testing

Tadalafil for Treatment of Priapism in Men With Sickle Cell Anemia

Who this might be right for
Sickle Cell AnemiaPriapism
Johns Hopkins University
Post-approval studies (Phase 4)Looking for participantsNCT06526117
What this trial is testing

Stroke Prevention in Nigeria 2 Trial

Who this might be right for
Sickle Cell DiseaseStroke
Vanderbilt University Medical Center 220
Not applicableUnknownNCT04432168
What this trial is testing

The TAPS Trial - Fetoscopic Laser Surgery for Twin Anemia Polycythemia Sequence

Who this might be right for
Twin Anemia Polycythemia Sequence
Leiden University Medical Center 44
Not applicableEnded earlyNCT05315908
What this trial is testing

COVID-19 Testing in Underserved and Vulnerable Populations

Who this might be right for
Heart FailureCoronary Artery DiseaseCancer+5 more
Jesse Nodora 9,120
Testing effectiveness (Phase 2)Active Not RecruitingNCT06171217
What this trial is testing

Realizing Effectiveness Across Continents With Hydroxyurea

Who this might be right for
Sickle Cell DiseaseChildren
Children's Hospital Medical Center, Cincinnati 811
Not applicableLooking for participantsNCT04528355
What this trial is testing

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

Who this might be right for
Primary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+2 more
Paul Szabolcs 50
Testing effectiveness (Phase 2)Looking for participantsNCT01962415
What this trial is testing

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

Who this might be right for
Primary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+4 more
Paul Szabolcs 100
Not applicableLooking for participantsNCT04166526
What this trial is testing

A Pilot Study on Neuroimaging in SCD: Part of The Boston Consortium to Cure Sickle Cell Disease

Who this might be right for
Sickle Cell Disease
Boston Children's Hospital 8
Large-scale testing (Phase 3)Study completedNCT01019876
What this trial is testing

Risk-Adapted Allogeneic Stem Cell Transplantation For Mixed Donor Chimerism In Patients With Non-Malignant Diseases

Who this might be right for
Bone Marrow FailureOsteopetrosisFanconi Anemia+1 more
Columbia University 38
Testing effectiveness (Phase 2)Study completedNCT02672540
What this trial is testing

SANGUINATE for the Treatment of Vaso-occlusive Crisis (VOC) in Adult Sickle Cell Disease Patients

Who this might be right for
Anemia, Sickle Cell
Prolong Pharmaceuticals 34
Not applicableStudy completedNCT03029468
What this trial is testing

Computerized Cognitive Behavioral Therapy Assisted Life Management for Pain in Sickle Cell Disease

Who this might be right for
Sickle Cell DiseaseChronic Pain
University of Pittsburgh 74
Not applicableWithdrawnNCT06098755
What this trial is testing

The Sequestration of Holistic Stress Management Techniques for Adults

Who this might be right for
Stress, JobPTSDHypervigilance+24 more
Goddess Zena I. Jones
Testing effectiveness (Phase 2)Study completedNCT00578435
What this trial is testing

Allogeneic Bone Marrow Transplantation for the Treatment of Genetic Disorders of Erythropoiesis

Who this might be right for
Genetic DisordersSickle Cell Anemia
Memorial Sloan Kettering Cancer Center 25
Not applicableNot Yet RecruitingNCT07639008
What this trial is testing

Epidemiology of Invasive Bacterial Infections in Children With Sickle Cell Disease in France Between 2020 and 2025

Who this might be right for
Sickle Cell Disease (SCD)Invasive Bacterial Infections
Assistance Publique - Hôpitaux de Paris 350
Not applicableStudy completedNCT03368261
What this trial is testing

Epidemiology and Pathophysiological Mechanisms of HTAP in SS and SC Children in Martinique and Guadeloupe.

Who this might be right for
Sickle Cell Disease
Centre Hospitalier Universitaire de la Guadeloupe 185
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