Large-scale testing (Phase 3)Study completedNCT00606060What this trial is testingBAY14-2222 Continuous Infusion in SurgeriesWho this might be right forHemophilia Bayer 15
Not applicableEnrolling By InvitationNCT07163260What this trial is testingDefeat Rare Disease in Asia and Pacific (APAC) DRDA - HaemophiliaWho this might be right forHaemophilia Novo Nordisk A/S 244
Not applicableStudy completedNCT02326597What this trial is testingDecision Aid for Therapeutic Options In Sickle Cell DiseaseWho this might be right forSickle Cell DiseaseSickle Cell AnemiaHemoglobin SS+2 more Emory University 134
Not applicableEnded earlyNCT04207320What this trial is testingHaploidentical Hematopoietic Stem Cell Transplantation (HSCT) for Patients With Severe Sickle Cell DiseaseWho this might be right forSickle Cell Disease University of Chicago 3
Large-scale testing (Phase 3)Ended earlyNCT00324324What this trial is testingMoxifloxacin in Preventing Bacterial Infections in Patients Who Have Undergone Donor Stem Cell TransplantWho this might be right forBreast CancerChronic Myeloproliferative DisordersGestational Trophoblastic Tumor+9 more OHSU Knight Cancer Institute 240
Testing effectiveness (Phase 2)Study completedNCT00001749What this trial is testingMedical Treatment for Diamond Blackfan AnemiaWho this might be right forFanconi's AnemiaHematologic Disease National Heart, Lung, and Blood Institute (NHLBI) 25
Testing effectiveness (Phase 2)Study completedNCT00445978What this trial is testingThe Effects of 6R-BH4 in Subjects With Sickle Cell DiseaseWho this might be right forSickle Cell Disease BioMarin Pharmaceutical 32
Not applicableUnknownNCT06276608What this trial is testingIron Deficiency in Pediatric Heart SurgeryWho this might be right forIron DeficienciesIron Deficiency AnemiaCardiac Surgical Procedures+1 more Queen Fabiola Children's University Hospital 300
Not applicableUnknownNCT02324517What this trial is testingEx Vivo Laboratory Assays Application for Therapy Tailoring in Patients With Severe Bleeding DisordersWho this might be right forSevere Hemophilia Sheba Medical Center 300
Not applicableUnknownNCT01403740What this trial is testingTurkish Acquired Haemophilia RegistryWho this might be right forAcquired Haemophilia Turkish Society of Hematology 250
Not applicableUnknownNCT03946384What this trial is testingMutation p.Ile112Thr : Discrepancy Between Factor IX Level and Bleeding PhenotypeWho this might be right forHemophilia B Centre Hospitalier Universitaire Dijon 12
Not applicableLooking for participantsNCT04463316What this trial is testingGROWing Up With Rare GENEtic SyndromesWho this might be right forPrader-Willi SyndromePWS-like SyndromeSilver Russel Syndrome+30 more dr. Laura C. G. de Graaff-Herder 600
Testing effectiveness (Phase 2)Ended earlyNCT04046848What this trial is testingSafety and Pharmacokinetics of Subcutaneous Injection of OCTA101 in Adult Patients With Severe Hemophilia AWho this might be right forSevere Hemophilia A Octapharma 36
Large-scale testing (Phase 3)Study completedNCT01963143What this trial is testingBioequivalence Study to Evaluate the Pharmacokinetics, Safety, and Tolerability of Gammaplex® 10 and Gammaplex® 5% in Primary Immunodeficiency DiseasesWho this might be right forPrimary Immune Deficiency DisordersCommon Variable ImmunodeficiencyX-linked Agammaglobulinaemia+1 more Bio Products Laboratory 48
Post-approval studies (Phase 4)Active Not RecruitingNCT05181618What this trial is testingEvaluate Overall Health, Physical Activity, and Joint Outcomes in Participants With Severe or Moderate Hemophilia A Without Factor VIII Inhibitors on Emicizumab ProphylaxisWho this might be right forSevere Hemophilia AModerate Hemophilia A Hoffmann-La Roche 136
Not applicableStudy completedNCT04364685What this trial is testingEffect of Walking on Sand With Dietary Intervention in Overweight Type 2 Diabetes Mellitus Patients.Who this might be right forWalking, DifficultyDiabetes Mellitus, Type 2Hemoglobin; Hb-SC Majmaah University 66
Not applicableLooking for participantsNCT06735625What this trial is testingPilot Study "AHSP as a Biomarker of Sickle Cell Disease in a Population of Adults and Children"Who this might be right forin Relation to Sickle Cell Disease Centre Hospitalier de Saint-Denis 100
Not applicableActive Not RecruitingNCT04406818What this trial is testingMetabolic and Hemodynamic Reserve in Pediatric SCAWho this might be right forChild, OnlyBrain DiseasesSickle Cell Disease+1 more Washington University School of Medicine 120
Not applicableStudy completedNCT04244240What this trial is testingLinks Between Cognitive Functions and Clinical, Biological and Neuroradiological Outcomes in Adults With Sickle Cell Disease.Who this might be right forSickle Cell DiseaseDrepanocytosis Hospices Civils de Lyon 19
Testing effectiveness (Phase 2)WithdrawnNCT01948817What this trial is testingDeferasirox BID (Twice a Day) in Transfusion Dependent Thalassemia Patients With Inadequate Response to High DosesWho this might be right forFocus on Transfusion Dependent Thalassemia Patients Who Are Inadequate Responders to Deferasirox > 35mg/kgQD Novartis Pharmaceuticals