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Results for “Congenital Marrow Failure”

220 trials

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Showing 20 of 220 results

Not applicableActive Not RecruitingNCT03047746
What this trial is testing

Unrelated And Partially Matched Related Donor PSCT w/ T Cell Receptor (TCR) αβ Depletion for Patients With BMF

Who this might be right for
Acquired Aplastic AnemiaParoxysmal Nocturnal HemoglobinuriaInherited Bone Marrow Failure Syndromes
Children's Hospital of Philadelphia 50
Testing effectiveness (Phase 2)Study completedNCT05828108
What this trial is testing

Study of the Selective GlyT1 Inhibitor Bitopertin for Steroid-Refractory Diamond-Blackfan Anemia

Who this might be right for
Steroid-refractory Diamond-Blackfan Anemia (DBA)
National Heart, Lung, and Blood Institute (NHLBI) 15
Testing effectiveness (Phase 2)Study completedNCT01020968
What this trial is testing

Use of Ixmyelocel-T (Formerly Catheter-based Cardiac Repair Cell [CRC]) Treatment in Patients With Heart Failure Due to Dilated Cardiomyopathy

Who this might be right for
Dilated Cardiomyopathy
Vericel Corporation 22
Early research (Phase 1)Study completedNCT00243399
What this trial is testing

Oxandrolone for the Treatment of Bone Marrow Aplasia in Fanconi Anemia

Who this might be right for
Fanconi Anemia
Children's Hospital Medical Center, Cincinnati 10
Early research (Phase 1)Study completedNCT00093743
What this trial is testing

Low-Dose Total-Body Irradiation and Fludarabine Phosphate Followed by Unrelated Donor Stem Cell Transplant in Treating Patients With Fanconi Anemia

Who this might be right for
Adult Acute Myeloid Leukemia in RemissionAdult Acute Myeloid Leukemia With 11q23 (MLL) AbnormalitiesAdult Acute Myeloid Leukemia With Del(5q)+8 more
Fred Hutchinson Cancer Center 2
Not applicableStudy completedNCT00244010
What this trial is testing

Partially Matched Stem Cell Transplantation for Patients With Refractory Severe Aplastic Anemia or Refractory Cytopenias

Who this might be right for
Anemia, AplasticAmegakaryocytic ThrombocytopeniaDiamond-Blackfan Anemia+1 more
St. Jude Children's Research Hospital 4
Testing effectiveness (Phase 2)Study completedNCT02678533
What this trial is testing

Mobilization and Collection of Peripheral Blood Stem Cells in Patients With Fanconi Anemia Using G-CSF and Plerixafor

Who this might be right for
Fanconi Anemia
Assistance Publique - Hôpitaux de Paris 4
Testing effectiveness (Phase 2)UnknownNCT04069533
What this trial is testing

Lentiviral-mediated Gene Therapy for Pediatric Patients With Fanconi Anemia Subtype A

Who this might be right for
Fanconi Anemia Complementation Group A
Rocket Pharmaceuticals Inc. 7
Large-scale testing (Phase 3)Study completedNCT00176878
What this trial is testing

Stem Cell Transplant for Bone Marrow Failure Syndromes

Who this might be right for
Diamond-Blackfan AnemiaKostmann's NeutropeniaShwachman-Diamond Syndrome
Masonic Cancer Center, University of Minnesota 10
Testing effectiveness (Phase 2)Study completedNCT03398824
What this trial is testing

Pilot Study of Metformin for Patients With Fanconi Anemia

Who this might be right for
Fanconi Anemia
Boston Children's Hospital 15
Testing effectiveness (Phase 2)Study completedNCT00777231
What this trial is testing

Phase I/II Pilot Study of Mixed Chimerism to Treat Hemoglobinopathies

Who this might be right for
Sickle Cell Disease
Talaris Therapeutics Inc. 9
Testing effectiveness (Phase 2)Ended earlyNCT02512679
What this trial is testing

Related Hematopoietic Stem Cell Transplantation (HSCT) for Genetic Diseases of Blood Cells

Who this might be right for
Stem Cell TransplantationBone Marrow TransplantationPeripheral Blood Stem Cell Transplantation+10 more
Children's Hospital Los Angeles 20
Not applicableStudy completedNCT00900055
What this trial is testing

Research Study in Healthy Volunteers of Patients With Fanconi Anemia, Myeloproliferative Disorders, or Myeloma

Who this might be right for
Chronic Myeloproliferative DisordersFanconi AnemiaMultiple Myeloma and Plasma Cell Neoplasm+1 more
OHSU Knight Cancer Institute 213
Testing effectiveness (Phase 2)Looking for participantsNCT04099966
What this trial is testing

AlloSCT for Malignant and Non-malignant Hematologic Diseases Utilizing Alpha/Beta T Cell and CD19+ B Cell Depletion

Who this might be right for
Acute LeukemiaSevere Aplastic AnemiaNon-hodgkin Lymphoma+6 more
Mitchell Cairo 20
Testing effectiveness (Phase 2)Ended earlyNCT00358657
What this trial is testing

Fludarabine Phosphate, Cyclophosphamide, and Total-Body Irradiation Followed by Donor Bone Marrow Transplant and Cyclophosphamide, Mycophenolate Mofetil, Tacrolimus, and Sirolimus in Treating Patients With Primary Immunodeficiency Disorders or Noncancerous Inherited Disorders

Who this might be right for
Immunodeficiency SyndromeSevere Aplastic AnemiaGenetic Disorder
Fred Hutchinson Cancer Center 14
Testing effectiveness (Phase 2)Study completedNCT06045052
What this trial is testing

Eltrombopag for Treatment of Fanconi Anemia

Who this might be right for
Fanconi Anemia
Julian Sevilla 8
Not applicableLooking for participantsNCT02720679
What this trial is testing

Investigation of the Genetics of Hematologic Diseases

Who this might be right for
Bone Marrow Failure SyndromesErythrocyte DisorderLeukocyte Disorder+10 more
St. Jude Children's Research Hospital 1,716
Early research (Phase 1)Study completedNCT00692926
What this trial is testing

Unrelated Umbilical Cord Blood Transplantation Augmented With ALDHbr Umbilical Cord Blood Cells

Who this might be right for
MDSAnemia, AplasticInborn Errors of Metabolism+2 more
Joanne Kurtzberg, MD 37
Post-approval studies (Phase 4)Study completedNCT00673608
What this trial is testing

Magnetic Resonance Imaging (MRI) Assessments of the Heart and Liver Iron Load in Patients With Transfusion Induced Iron Overload

Who this might be right for
HemoglobinopathiesMyelodysplastic SyndromesOther Inherited or Acquired Anaemia+4 more
Novartis 118
Not applicableStudy completedNCT01758042
What this trial is testing

Bone Marrow and Kidney Transplant for Patients With Chronic Kidney Disease and Blood Disorders

Who this might be right for
Chronic Kidney DiseaseAcute Myeloid Leukemia (AML)Acute Lymphoblastic Leukemia (ALL)+14 more
Massachusetts General Hospital 10
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