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Results for “Congenital Marrow Failure”

216 trials

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Showing 20 of 216 results

Testing effectiveness (Phase 2)Looking for participantsNCT04356469
What this trial is testing

TCR Alpha Beta T-cell Depleted Haploidentical HCT in the Treatment of Non-Malignant Hematological Disorders in Children

Who this might be right for
Hemoglobinopathy (Disorder)Severe Aplastic AnemiaBone Marrow Failure Syndrome
Johns Hopkins All Children's Hospital 17
Early research (Phase 1)Study completedNCT00243399
What this trial is testing

Oxandrolone for the Treatment of Bone Marrow Aplasia in Fanconi Anemia

Who this might be right for
Fanconi Anemia
Children's Hospital Medical Center, Cincinnati 10
Testing effectiveness (Phase 2)Study completedNCT00002809
What this trial is testing

Bone Marrow Transplant Plus Cyclophosphamide and Total-Body Irradiation in Treating Patients With Hematologic Cancer

Who this might be right for
LeukemiaMyelodysplastic SyndromesMyelodysplastic/Myeloproliferative Diseases
Temple University 10
Testing effectiveness (Phase 2)Ended earlyNCT01596699
What this trial is testing

Pilot Trial of Clofarabine Added to Standard Busulfan and Fludarabine for Conditioning Prior to Allogeneic Hematopoietic Cell Transplantation

Who this might be right for
Myeloid MalignancyBone Marrow Failure SyndromeTransfusion-dependent Red Blood Cell (RBC) Defect+3 more
University of California, San Francisco 16
Not applicableStudy completedNCT02479776
What this trial is testing

A Trial of Autologous Bone Marrow Derived Stem Cells in Paediatric Heart Failure

Who this might be right for
Dilated Cardiomyopathy
Great Ormond Street Hospital for Children NHS Foundation Trust 10
Not applicableLooking for participantsNCT04781790
What this trial is testing

French National Registry of Bone Marrow Failures

Who this might be right for
Bone Marrow Failure Syndrome
Assistance Publique - Hôpitaux de Paris 5,000
Large-scale testing (Phase 3)Study completedNCT00235391
What this trial is testing

Expanded Access of Deferasirox to Patients With Congenital Disorders of Red Blood Cells and Chronic Iron Overload

Who this might be right for
ThalassemiaSickle Cell DiseaseDiamond Blackfan Anemia+1 more
Novartis Pharmaceuticals 1,683
Testing effectiveness (Phase 2)Study completedNCT00004143
What this trial is testing

Allogeneic Mixed Chimerism Stem Cell Transplant Using Campath for Hemoglobinopathies & Bone Marrow Failure Syndromes

Who this might be right for
Sickle Cell AnemiaSevere Aplastic AnemiaParoxysmal Nocturnal Hemoglobinuria (PNH)+1 more
David Rizzieri, MD 2
Testing effectiveness (Phase 2)Study completedNCT03513328
What this trial is testing

Conditioning Regimen for Allogeneic Hematopoietic Stem-Cell Transplantation

Who this might be right for
Bone Marrow Failure SyndromeThalassemiaSickle Cell Disease+13 more
University of Florida 6
Not applicableLooking for participantsNCT06056908
What this trial is testing

Shwachman Diamond Syndrome Registry and Study

Who this might be right for
Shwachman-Diamond SyndromeShwachman-Diamond Syndrome-Like
Boston Children's Hospital 5,000
Testing effectiveness (Phase 2)Study completedNCT00479115
What this trial is testing

Mobilization and Collection of Peripheral Blood Stem Cells in Patients With Fanconi Anemia Using G-CSF and AMD3100

Who this might be right for
Fanconi Anemia
Children's Hospital Medical Center, Cincinnati 1
Not applicableStudy completedNCT05298930
What this trial is testing

Feasibility Study to Assess an Adapted Physical Activity Program in Children, Adolescents and Young Adults Requiring Hematopoietic Stem Cell Transplantation

Who this might be right for
Haematological MalignancyAcute LeukemiaMyelodysplastic Syndromes+3 more
Centre Leon Berard 15
Testing effectiveness (Phase 2)Study completedNCT00229619
What this trial is testing

Rituximab to Treat Moderate Aplastic Anemia, Pure Red Cell Aplasia, or Diamond Blackfan Anemia

Who this might be right for
Anemia, AplasticRed-Cell Aplasia, PureAnemia, Diamond-Blackfan
National Heart, Lung, and Blood Institute (NHLBI) 11
Not applicableAvailableNCT01881334
What this trial is testing

Expanded Access to T-cell Depleted Haplo-Identical Stem Cells for Patients Receiving Haplo-Identical and Unrelated Cord Blood Transplants

Who this might be right for
Hematologic MalignanciesInborn Errors of Metabolism DisordersImmune Deficiencies
Joanne Kurtzberg, MD
Large-scale testing (Phase 3)Study completedNCT00171821
What this trial is testing

A Study Assessing the Efficacy and Safety of Deferasirox in Patients With Transfusion-dependent Iron Overload

Who this might be right for
Transfusion-dependent Iron Overload
Novartis Pharmaceuticals 1,784
Not applicableStudy completedNCT03609814
What this trial is testing

Study of Clofarabine and Fludarabine Drug Exposure in Pediatric Bone Marrow Transplantation (HCT)

Who this might be right for
Hematologic MalignanciesNonmalignant DiseasesImmunodeficiencies+5 more
University of California, San Francisco 30
Testing effectiveness (Phase 2)Study completedNCT01362595
What this trial is testing

Pilot Phase I/II Study of Amino Acid Leucine in Treatment of Patients With Transfusion-Dependent Diamond Blackfan Anemia

Who this might be right for
Diamond Blackfan AnemiaBlackfan Diamond SyndromeDBA+2 more
Northwell Health 55
Not applicableNo Longer AvailableNCT01200017
What this trial is testing

Expanded Access Protocol (EAP) Using the CliniMACS® Device for Pediatric Haplocompatible Donor Stem Cell Transplant

Who this might be right for
Acute Lymphoblastic LeukemiaAcute Myeloid LeukemiaChronic Myeloid Leukemia+9 more
Christopher Dvorak
Not applicableNot Yet RecruitingNCT07227155
What this trial is testing

The HOPE Biobank Resource (BMT CTN 2402 HOPE)

Who this might be right for
Aplastic AnemiasHemoglobinopathiesBone Marrow Failure
Medical College of Wisconsin 375
Testing effectiveness (Phase 2)Ended earlyNCT03966053
What this trial is testing

The Use of Trifluoperazine in Transfusion Dependent DBA

Who this might be right for
Diamond Blackfan AnemiaPure Red Cell Aplasia
Adrianna Vlachos, MD 2
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