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Results for “Congenital Marrow Failure”

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Showing 20 of 0 results

Testing effectiveness (Phase 2)Study completedNCT00001749
What this trial is testing

Medical Treatment for Diamond Blackfan Anemia

Who this might be right for
Fanconi's AnemiaHematologic Disease
National Heart, Lung, and Blood Institute (NHLBI) 25
Not applicableLooking for participantsNCT07145411
What this trial is testing

HPC Offered for PRESERVE Expansion

Who this might be right for
Bone Marrow Transplant (BMT)
Ossium Health, Inc. 10
Testing effectiveness (Phase 2)WithdrawnNCT01419704
What this trial is testing

Phase I/II Pilot Study of Mixed Chimerism to Treat Hemoglobinopathies

Who this might be right for
Anemia, Sickle CellComplex and Transfusion-dependent HemoglobinopathiesThalassemia+4 more
Talaris Therapeutics Inc.
Not applicableLooking for participantsNCT06250595
What this trial is testing

European Rare Blood Disorders Platform (ENROL)

Who this might be right for
AnemiaBone Marrow FailureBleeding Disorder+9 more
Hospital Universitari Vall d'Hebron Research Institute 37,090
Not applicableStudy completedNCT05298930
What this trial is testing

Feasibility Study to Assess an Adapted Physical Activity Program in Children, Adolescents and Young Adults Requiring Hematopoietic Stem Cell Transplantation

Who this might be right for
Haematological MalignancyAcute LeukemiaMyelodysplastic Syndromes+3 more
Centre Leon Berard 15
Testing effectiveness (Phase 2)Not Yet RecruitingNCT07408583
What this trial is testing

Prenatal Transplantation for Fetuses With Fanconi Anemia

Who this might be right for
Fanconi AnemiaAnemia, Hypoplastic, CongenitalCongenital Bone Marrow Failure Syndromes+5 more
Agnieszka Czechowicz 12
Large-scale testing (Phase 3)Study completedNCT00755040
What this trial is testing

Cyclosporine Eye Drops in Preventing Graft-Versus-Host Disease of the Eye in Patients Who Have Undergone Donor Stem Cell Transplant for Hematologic Cancer or Bone Marrow Failure Disorder

Who this might be right for
Chronic Myeloproliferative DisordersGraft Versus Host DiseaseLeukemia+4 more
Vanderbilt-Ingram Cancer Center 164
Testing effectiveness (Phase 2)UnknownNCT02061800
What this trial is testing

CD34+ (Malignant) Stem Cell Selection for Patients Receiving Allogenic Stem Cell Transplant

Who this might be right for
Chronic Myeloid Leukemia (CML)Acute Myelogenous Leukemia (AML)Myelodysplastic Syndrome (MDS)+3 more
Diane George 14
Not applicableLooking for participantsNCT06689800
What this trial is testing

Let's Get REAL: Family Health Communication Tool in Pediatric Stem Cell Transplant and Cellular Therapy

Who this might be right for
Hematologic MalignancySolid TumorSickle Cell Disease+3 more
Washington University School of Medicine 60
Not applicableLooking for participantsNCT04528355
What this trial is testing

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

Who this might be right for
Primary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+2 more
Paul Szabolcs 50
Testing effectiveness (Phase 2)Looking for participantsNCT01962415
What this trial is testing

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

Who this might be right for
Primary Immunodeficiency (PID)Congenital Bone Marrow Failure SyndromesInherited Metabolic Disorders (IMD)+4 more
Paul Szabolcs 100
Not applicableStudy completedNCT00271089
What this trial is testing

Blood Cell Collection for Future Use in Individuals With Fanconi Anemia

Who this might be right for
Fanconi Anemia
National Heart, Lung, and Blood Institute (NHLBI) 40
Not applicableStudy completedNCT00005893
What this trial is testing

Study of Allogeneic Bone Marrow Transplantation Using Matched, Related Donors in Patients With Nonmalignant Hematologic Disorders

Who this might be right for
NeutropeniaSickle Cell AnemiaThalassemia Major+1 more
Fairview University Medical Center
Early research (Phase 1)Looking for participantsNCT06090669
What this trial is testing

Imatinib to Increase RUNX1 Activity in Participants With Germline RUNX1 Deficiency

Who this might be right for
Inherited Bone Marrow Failure SyndromeFamilial Platelet Disorder With Predisposition to Myeloid Malignancies
National Cancer Institute (NCI) 75
Testing effectiveness (Phase 2)Study completedNCT01044186
What this trial is testing

A Protocol to Allow Treatment With ICL670 for Patients With or at Risk of Life-threatening Complications of Transfusional Iron Overload Who Are Unable to Tolerate Other Iron Chelators Because of Documented Severe Toxicity

Who this might be right for
Transfusional Iron Overload
Novartis Pharmaceuticals 30
Testing effectiveness (Phase 2)Study completedNCT01224496
What this trial is testing

Traditional Chinese Medicine in the Supportive Management of Anaemic and Cytopenic (Leukopenia, Thrombocytopenia) Haematological Disorders

Who this might be right for
Myelodysplastic Syndrome (MDS)Aplastic Anaemia (AA)Myelofibrosis (MF)+1 more
Singapore General Hospital 38
Not applicableLooking for participantsNCT06056908
What this trial is testing

Shwachman Diamond Syndrome Registry and Study

Who this might be right for
Shwachman-Diamond SyndromeShwachman-Diamond Syndrome-Like
Boston Children's Hospital 5,000
Not applicableStudy completedNCT00964821
What this trial is testing

Flu Vaccine in Preventing Influenza Infection in Healthy Volunteers and in Patients Who Have Undergone Stem Cell Transplant

Who this might be right for
Chronic Myeloproliferative DisordersLeukemiaLymphoma+4 more
City of Hope Medical Center 459
Testing effectiveness (Phase 2)Study completedNCT01362595
What this trial is testing

Pilot Phase I/II Study of Amino Acid Leucine in Treatment of Patients With Transfusion-Dependent Diamond Blackfan Anemia

Who this might be right for
Diamond Blackfan AnemiaBlackfan Diamond SyndromeDBA+2 more
Northwell Health 55
Not applicableStudy completedNCT03609814
What this trial is testing

Study of Clofarabine and Fludarabine Drug Exposure in Pediatric Bone Marrow Transplantation (HCT)

Who this might be right for
Hematologic MalignanciesNonmalignant DiseasesImmunodeficiencies+5 more
University of California, San Francisco 30
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