Not applicableLooking for participantsNCT03466463What this trial is testingGene Therapy for Severe Crigler Najjar SyndromeWho this might be right forCrigler-Najjar Syndrome Genethon 17
Testing effectiveness (Phase 2)Looking for participantsNCT06641154What this trial is testingGene Therapy for Crigler Najjar Syndrome Type I (AlphaCN)Who this might be right forCrigler-Najjar Syndrome Type I Federal State Budget Institution Research Center for Obstetrics, Gynecology and Perinatology Ministry of Healthcare 5
Early research (Phase 1)Ended earlyNCT03223194What this trial is testingGene Transfer Clinical Study in Crigler-Najjar SyndromeWho this might be right forCrigler-Najjar Syndrome Audentes Therapeutics 1
Testing effectiveness (Phase 2)Looking for participantsNCT06518005What this trial is testingEfficacy and Safety of GNT0003 Following Imlifidase Pre-treatment in Severe Crigler-Najjar SyndromeWho this might be right forCrigler-Najjar Syndrome Genethon 3
Not applicableEnded earlyNCT03343756What this trial is testingHepaStem Long-Term Safety RegistryWho this might be right forUrea Cycle DisorderCrigler-Najjar SyndromeAcute on Chronic Liver Failure Cellaion SA 44
Not applicableStudy completedNCT05687474What this trial is testingBaby Detect : Genomic Newborn ScreeningWho this might be right forCongenital Adrenal HyperplasiaFamilial Hyperinsulinemic Hypoglycemia 1Phosphoglucomutase 1 Deficiency+121 more Centre Hospitalier Universitaire de Liege 6,824
Not applicableStudy completedNCT00461799What this trial is testingOrlistat Treatment of Crigler-Najjar DiseaseWho this might be right forCrigler-Najjar Syndrome University Medical Center Groningen 16
Not applicableUnknownNCT02356978What this trial is testingNew Phototherapy Device to Treat Patients With Crigler-Najjar DiseaseWho this might be right forCrigler Najjar SyndromeChildren Assistance Publique - Hôpitaux de Paris 6
Not applicableStudy completedNCT03078881What this trial is testingClinical Assessment Study in Crigler-Najjar SyndromeWho this might be right forCrigler-Najjar Syndrome Audentes Therapeutics 8
Early research (Phase 1)Ended earlyNCT01345578What this trial is testingHepatocyte Transplantation for Liver Based Metabolic DisordersWho this might be right forMetabolic Diseases Ira Fox 5
Not applicableStudy completedNCT02302690What this trial is testingImmunity Against AAV in Crigler Najjar PatientWho this might be right forCrigler Najjar Syndrome Genethon 49
Not applicableStudy completedNCT02051049What this trial is testingLong-term Safety Follow-up Study of Patients Having Received HepaStem (SAF001)Who this might be right forUrea Cycle DisordersCrigler Najjar Syndrome Cellaion SA 9
Testing effectiveness (Phase 2)Study completedNCT01765283What this trial is testingSafety Study of HepaStem for the Treatment of Urea Cycle Disorders (UCD) and Crigler-Najjar Syndrome (CN)Who this might be right forUrea Cycle DisordersCrigler Najjar Syndrome Cellaion SA 20