Not applicableLooking for participantsNCT06214507What this trial is testingDanon Disease Natural History StudyWho this might be right forDanon Disease Rocket Pharmaceuticals Inc. 60
Not applicableLooking for participantsNCT06795152What this trial is testingRare Glycogen Storage Diseases Natural History StudyWho this might be right forGlycogen Storage DiseaseGSD Type 0AGSD Type 0B+12 more Duke University 200
Not applicableStudy completedNCT05548855What this trial is testingNatural History of Danon DiseaseWho this might be right forDanon Disease Rocket Pharmaceuticals Inc. 59
Early research (Phase 1)UnknownNCT03882437What this trial is testingGene Therapy for Male Patients With Danon Disease (DD) Using RP-A501; AAV9.LAMP2BWho this might be right forDanon Disease Rocket Pharmaceuticals Inc. 7
Not applicableLooking for participantsNCT07336394What this trial is testingPrecision Diagnosis and Risk Stratification of Rare Cardiomyopathies Based on Novel Cardiac Magnetic Resonance TechniquesWho this might be right forDanon DiseaseFabry DiseaseCardiac Amyloidosis+4 more Chinese Academy of Medical Sciences, Fuwai Hospital 1,000
Not applicableUnknownNCT03766386What this trial is testingThe Natural History of Danon DiseaseWho this might be right forDanon Disease University of California, San Diego 200
Testing effectiveness (Phase 2)Looking for participantsNCT06092034What this trial is testingA Gene Therapy Study of RP-A501 in Male Patients With Danon DiseaseWho this might be right forDanon Disease Rocket Pharmaceuticals Inc. 14