Not applicableLooking for participantsNCT05489393What this trial is testingCureDRPLA Global Patient RegistryWho this might be right forDRPLA CureDRPLA 100
Testing effectiveness (Phase 2)Active Not RecruitingNCT06706388What this trial is testingPersonalized Antisense Oligonucleotide Therapy for A Single Participant With ATN1 Gene MutationWho this might be right forDentatorubral-Pallidoluysian Atrophy n-Lorem Foundation 1
Not applicableUnknownNCT06273150What this trial is testingDentatorubral-pallidoluysian Atrophy Natural History and Biomarkers StudyWho this might be right forDentatorubral-Pallidoluysian Atrophy University College, London 225
Testing effectiveness (Phase 2)Active Not RecruitingNCT07221760What this trial is testingPersonalized Antisense Oligonucleotide for A Single Participant (nL62541) With ATN1 Gene MutationWho this might be right forDentatorubral-Pallidoluysian Atrophy n-Lorem Foundation 1
Testing effectiveness (Phase 2)Active Not RecruitingNCT07084311What this trial is testingPersonalized Antisense Oligonucleotide for A Single Participant With ATN1 Gene MutationWho this might be right forDentatorubral-Pallidoluysian Atrophy n-Lorem Foundation 1