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Results for “Enzyme Disorder; Anemia”

16 trials

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Showing 16 of 16 results

Not applicableUnknownNCT03805776
What this trial is testing

Intermittent Fasting in Dyslipidemia

Who this might be right for
Intermittent FastingDyslipidemiasHDL Cholesterol, Low Serum+4 more
Aga Khan University 60
Early research (Phase 1)Study completedNCT00261274
What this trial is testing

Safety Study of ECO Conversion System For Red Blood Cells.

Who this might be right for
Anemia
Velico Medical 60
Testing effectiveness (Phase 2)Study completedNCT00004997
What this trial is testing

Leucovorin for the Treatment of 5 q Minus Syndrome

Who this might be right for
5q Minus SyndromeMyelodysplastic Syndrome
National Institutes of Health Clinical Center (CC) 14
Not applicableStudy completedNCT06831799
What this trial is testing

ERN-EuroBloodNet Registry on Patients With Rare Red Blood Cell Defects and COVID-19

Who this might be right for
HemoglobinopathiesSickle Cell DiseaseSickle Cell Anemia+21 more
Hospital Universitari Vall d'Hebron Research Institute 684
Not applicableLooking for participantsNCT07206095
What this trial is testing

Integrative Diagnosis for SCD and Other RADs

Who this might be right for
Sickle Cell DiseaseThalassaemiaCongenital Dyserythropoietic Anemia (CDA)+6 more
Hospital Universitari Vall d'Hebron Research Institute 200
Not applicableStudy completedNCT00593801
What this trial is testing

Erythropoietin Treatment in Extremely Low Birth Weight Infants

Who this might be right for
Infant, Low Birth WeightAnemia
Charite University, Berlin, Germany 219
Not applicableStudy completedNCT04995315
What this trial is testing

Pyruvate Kinase Deficiency Global Longitudinal Registry Substudy of Protocol AG348-C-008

Who this might be right for
Pyruvate Kinase Deficiency
Agios Pharmaceuticals, Inc. 13
Not applicableNo Longer AvailableNCT00962260
What this trial is testing

Expanded Access Trial of Plant Expressed Recombinant Glucocerebrosidase (prGCD) in Patients With Gaucher Disease

Who this might be right for
Gaucher Disease
Pfizer
Not applicableStudy completedNCT02053480
What this trial is testing

Pyruvate Kinase Deficiency Natural History Study

Who this might be right for
Pyruvate Kinase DeficiencyCongenital Non-Spherocytic Hemolytic Anemia
Boston Children's Hospital 254
Not applicableEnded earlyNCT01096121
What this trial is testing

Angiotensin-converting Enzyme Inhibitors and Early Sickle Cell Renal Disease in Children

Who this might be right for
Sickle Cell Disease
Assistance Publique - Hôpitaux de Paris 5
Not applicableActive Not RecruitingNCT03481738
What this trial is testing

Pyruvate Kinase Deficiency Global Longitudinal Registry

Who this might be right for
Pyruvate Kinase Deficiency
Agios Pharmaceuticals, Inc. 500
Not applicableLooking for participantsNCT06213402
What this trial is testing

RADeep Multicenter European Epidemiological Platform for Patients Diagnosed With Rare Anemia Disorders (RADs)

Who this might be right for
Sickle Cell DiseaseThalassemiaHemolytic; Anemia, Hereditary, Due to Enzyme Disorder+6 more
Hospital Universitari Vall d'Hebron Research Institute 32,564
Post-approval studies (Phase 4)UnknownNCT06115421
What this trial is testing

Effect of Low Doses of Hypoxia-inducible Factor- Prolyl Hydroxylase Enzyme Inhibitor Plus Iron in the Treatment of Anemia in Dialysis-dependent Chronic Kidney Disease Patients

Who this might be right for
Anemia in Dialysis-dependent CKD Patients
Alexandria University 72
Not applicableLooking for participantsNCT06250595
What this trial is testing

European Rare Blood Disorders Platform (ENROL)

Who this might be right for
AnemiaBone Marrow FailureBleeding Disorder+9 more
Hospital Universitari Vall d'Hebron Research Institute 37,090
Not applicableEnded earlyNCT04964323
What this trial is testing

Pyruvate Kinase (PK) Deficiency Global Longitudinal Registry: Patient-Reported Outcomes (PRO)

Who this might be right for
Pyruvate Kinase DeficiencyPyruvate Kinase Deficiency AnemiaAnemia+1 more
Agios Pharmaceuticals, Inc. 15
Large-scale testing (Phase 3)Study completedNCT01414374
What this trial is testing

Hibiscus Sabdariffa and Centella Asiatica in the Treatment of Anemia by Iron Deficiency

Who this might be right for
Iron Deficiency Anemia
Casa Espirita Terra de Ismael 50