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Results for “Familial Amyloidotic Cardiomyopathy (FAC)”

2 trials

Showing 2 of 2 results

Large-scale testing (Phase 3)Study completedNCT02319005
What this trial is testing

ENDEAVOUR: Phase 3 Multicenter Study of Revusiran (ALN-TTRSC) in Patients With Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC)

Who this might be right for
Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC)Amyloidosis, HereditaryAmyloid Neuropathies, Familial+3 more
Alnylam Pharmaceuticals 206
Not applicableStudy completedNCT02252653
What this trial is testing

DISCOVERY: A Study Examining the Prevalence of TTR Mutations in Subjects Suspected of Having Cardiac Amyloidosis

Who this might be right for
Familial Amyloidotic Cardiomyopathy (FAC)
Alnylam Pharmaceuticals 1,010

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