Testing effectiveness (Phase 2)Study completedNCT02845609What this trial is testingEfficacy of Sialic Acid GNE Related ThrombocytopeniaWho this might be right forThrombocytopenia Hadassah Medical Organization 5
Not applicableStudy completedNCT01417533What this trial is testingA Natural History Study of Patients With GNE Myopathy and GNE-Related DiseasesWho this might be right forGNE MyopathyGNE Related Diseases National Human Genome Research Institute (NHGRI) 78