Not applicableNo Longer AvailableNCT01461304
What this trial is testing
Compassionate Use of Triheptanoin (C7) for Inherited Disorders of Energy Metabolism
Who this might be right for
Very Long-chain acylCoA Dehydrogenase (VLCAD) DeficiencyCarnitine Palmitoyltransferase Deficiencies (CPT1, CPT2)Mitochondrial Trifunctional Protein Deficiency+5 more
Jerry Vockley, MD, PhD