Large-scale testing (Phase 3)Study completedNCT02770625What this trial is testingPhase III Study of ISU302 in Patients With Type 1 Gaucher DiseaseWho this might be right forGaucher Disease, Type 1 ISU Abxis Co., Ltd. 8
Early research (Phase 1)Looking for participantsNCT03721068What this trial is testingStudy of CAR T-Cells Targeting the GD2 With IL-15+iCaspase9 for Relapsed/Refractory Neuroblastoma or Relapsed/Refractory OsteosarcomaWho this might be right forNeuroblastomaOsteosarcoma UNC Lineberger Comprehensive Cancer Center 18
Not applicableLooking for participantsNCT06162338What this trial is testingThe Safety and Preliminary Efficacy of LY-M001 Injection in the Treatment of Adult Patients With Gaucher Disease Type IWho this might be right forGaucher Disease Type I He Huang 3
Testing effectiveness (Phase 2)Temporarily pausedNCT01463215What this trial is testingClinical Trial of Ambroxol in Patients With Type I Gaucher DiseaseWho this might be right forType I Gaucher Disease Exsar Corporation 20
Testing effectiveness (Phase 2)Not Yet RecruitingNCT04637503What this trial is testing4SCAR-T Therapy Targeting GD2, PSMA and CD276 for Treating NeuroblastomaWho this might be right forNeuroblastoma Shenzhen Geno-Immune Medical Institute 100
Early research (Phase 1)Study completedNCT00004294What this trial is testingPhase I Study of Retrovirally Mediated Transfer of the Human Glucocerebrosidase Gene Into Peripheral Blood Stem Cells for Autologous Transplantation in Patients With Type I Gaucher DiseaseWho this might be right forGaucher's Disease National Center for Research Resources (NCRR) 15
Large-scale testing (Phase 3)Study completedNCT05529992What this trial is testingVelaglucerase Alfa (VPRIV) in Chinese Children, Teenagers, and Adults With Type 1 Gaucher DiseaseWho this might be right forGaucher Disease Takeda 20
Testing effectiveness (Phase 2)Study completedNCT00446550What this trial is testingOral AT2101 (Afegostat Tartrate) in Treatment-naive Patients With Gaucher DiseaseWho this might be right forGaucher DiseaseType 1 Gaucher DiseaseGaucher Disease, Type 1 Amicus Therapeutics 19
Large-scale testing (Phase 3)WithdrawnNCT01161914What this trial is testingThe Safety and Efficacy Study of ISU302 in Patient With Type I Gaucher DiseaseWho this might be right forGaucher Disease ISU Abxis Co., Ltd.
Large-scale testing (Phase 3)Study completedNCT00430625What this trial is testingGene-Activated® Human Glucocerebrosidase (GA-GCB) Enzyme Replacement Therapy in Gaucher DiseaseWho this might be right forGaucher Disease, Type 1 Shire 25
Large-scale testing (Phase 3)Study completedNCT03485677What this trial is testingSafety and Efficacy of Eliglustat With or Without Imiglucerase in Pediatric Patients With Gaucher Disease (GD) Type 1 and Type 3Who this might be right forGaucher's Disease Type IGaucher's Disease Type III Sanofi 57
Not applicableStudy completedNCT00351156What this trial is testingStudy to Evaluate Blood Cell Lines From Patients With Gaucher DiseaseWho this might be right forGaucher Disease Amicus Therapeutics 50
Early research (Phase 1)Study completedNCT05324943What this trial is testingA Gene Therapy Study in Patients With Gaucher Disease Type 1Who this might be right forGaucher Disease, Type 1 Spur Therapeutics 10
Post-approval studies (Phase 4)Study completedNCT02574286What this trial is testingStudy of the Effect of Velaglucerase Alfa (VPRIV®) on Bone-related Pathology in Treatment-naïve Participants With Type 1 Gaucher DiseaseWho this might be right forGaucher Disease Shire 21
Testing effectiveness (Phase 2)Active Not RecruitingNCT02843035What this trial is testingVenglustat in Combination With Cerezyme in Adult Patients With Gaucher Disease Type 3 With Venglustat Monotherapy ExtensionWho this might be right forGaucher Disease Type 1Gaucher Disease Type 3 Genzyme, a Sanofi Company 12
Early research (Phase 1)Ended earlyNCT00875160What this trial is testingA Study in Type 1 Gaucher Patients to Evaluate the Pharmacokinetics, Safety and Pharmacodynamics of AT2101Who this might be right forType 1 Gaucher Disease Amicus Therapeutics 1
Post-approval studies (Phase 4)Study completedNCT04718779What this trial is testingEnzyme Replacement Therapy (VPRIV) in People With Type 1 Gaucher Disease Who Were Previously Treated With Substrate Reduction TherapyWho this might be right forGaucher Disease Takeda 4
Not applicableWithdrawnNCT00795197What this trial is testingA Screening Study Evaluating Disease Status of Gaucher Type I PatientsWho this might be right forGaucher Disease, Type 1 Genzyme, a Sanofi Company
Testing effectiveness (Phase 2)Active Not RecruitingNCT05487599What this trial is testingA Clinical Trial of PR001 (LY3884961) in Patients With Peripheral Manifestations of Gaucher Disease (PROCEED)Who this might be right forGaucher DiseaseGaucher Disease, Type 1 Prevail Therapeutics 8
Large-scale testing (Phase 3)Study completedNCT00635427What this trial is testingAn Open-Label Extension Study of GA-GCB ERT in Patients With Type 1 Gaucher DiseaseWho this might be right forGaucher Disease, Type 1 Shire 95